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Muscle Gene Therapy最新文献

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Duchenne Muscular Dystrophy Exon-Skipping Trials 杜氏肌营养不良症外显子跳跃试验
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_42
J. Mendell, Z. Sahenk, L. Rodino-Klapac
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引用次数: 1
Dystroglycanopathy Gene Therapy: Unlocking the Potential of Genetic Engineering 糖代谢异常基因治疗:释放基因工程的潜力
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_27
C. Vannoy, A. Blaeser, Q. Lu
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引用次数: 0
Gene Therapy and Gene Editing for Myotonic Dystrophy 强直性肌营养不良症的基因治疗和基因编辑
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_30
M. Chuah, Y. C. Chai, Sumitava Dastidar, T. VandenDriessche
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引用次数: 1
Elimination of Mutant Mitochondrial DNA in Mitochondrial Myopathies Using Gene-Editing Enzymes 利用基因编辑酶消除线粒体肌病中的突变线粒体DNA
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_34
S. Bacman, C. Moraes
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引用次数: 0
Viral Vectors for Muscle Gene Therapy 肌肉基因治疗的病毒载体
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_10
Dan Wang, Alexander Brown, G. Gao
{"title":"Viral Vectors for Muscle Gene Therapy","authors":"Dan Wang, Alexander Brown, G. Gao","doi":"10.1007/978-3-030-03095-7_10","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_10","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"2 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"123270891","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Design of Clinical Trials for Gene Therapy in Muscular Dystrophy 肌萎缩症基因治疗的临床试验设计
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_38
J. Quiroz, K. Wagner
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引用次数: 0
Genome Editing for Duchenne Muscular Dystrophy 杜氏肌营养不良症的基因组编辑
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_22
Christopher E. Nelson, C. Gersbach
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引用次数: 4
Biomarkers for Muscle Disease Gene Therapy 肌肉疾病基因治疗的生物标志物
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_14
Y. Hathout, K. Brown, K. Nagaraju, E. Hoffman
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引用次数: 0
Muscle as a Potent Target in Vaccination 肌肉作为疫苗接种的有效靶点
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_36
Axel Rossi, H. Büning
{"title":"Muscle as a Potent Target in Vaccination","authors":"Axel Rossi, H. Büning","doi":"10.1007/978-3-030-03095-7_36","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_36","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"39 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"130618808","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Development of Next-Generation Muscle Gene Therapy AAV Vectors 新一代肌肉基因治疗AAV载体的研制
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_11
Michael E. Nance, D. Duan
{"title":"Development of Next-Generation Muscle Gene Therapy AAV Vectors","authors":"Michael E. Nance, D. Duan","doi":"10.1007/978-3-030-03095-7_11","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_11","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"17 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"116275525","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 1
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