Muscle Gene Therapy最新文献

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Therapeutic Approaches for Dysferlinopathy in Animal Models 动物模型中异ferlin病的治疗方法
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_25
W. Lostal, I. Richard
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引用次数: 0
Immune System Regulation of Muscle Injury and Disease 肌肉损伤和疾病的免疫系统调节
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_7
J. Kastenschmidt, Ali H. Mannaa, Karissa J. Muñoz, S. Villalta
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引用次数: 0
Recent Advances in AON-Mediated Exon-Skipping Therapy for Duchenne Muscular Dystrophy aon介导的外显子跳跃治疗杜氏肌营养不良的最新进展
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_19
Xianjun Gao, Gang Han, H. Yin
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引用次数: 1
Large-Scale Clinical Manufacturing of AAV Vectors for Systemic Muscle Gene Therapy 用于全身肌肉基因治疗的AAV载体的大规模临床生产
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_15
N. Clément
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引用次数: 5
MicroRNAs (miRs) in Muscle Gene Therapy 肌肉基因治疗中的MicroRNAs (miRs)
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_6
A. Rotini, Giorgia Giacomazzi, E. S. D. Filippo, M. Sampaolesi
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引用次数: 1
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