{"title":"Therapeutic Approaches for Dysferlinopathy in Animal Models","authors":"W. Lostal, I. Richard","doi":"10.1007/978-3-030-03095-7_25","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_25","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"7 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"133914060","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
J. Kastenschmidt, Ali H. Mannaa, Karissa J. Muñoz, S. Villalta
{"title":"Immune System Regulation of Muscle Injury and Disease","authors":"J. Kastenschmidt, Ali H. Mannaa, Karissa J. Muñoz, S. Villalta","doi":"10.1007/978-3-030-03095-7_7","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_7","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"24 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"131773394","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Recent Advances in AON-Mediated Exon-Skipping Therapy for Duchenne Muscular Dystrophy","authors":"Xianjun Gao, Gang Han, H. Yin","doi":"10.1007/978-3-030-03095-7_19","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_19","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"105 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129024487","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
A. Rotini, Giorgia Giacomazzi, E. S. D. Filippo, M. Sampaolesi
{"title":"MicroRNAs (miRs) in Muscle Gene Therapy","authors":"A. Rotini, Giorgia Giacomazzi, E. S. D. Filippo, M. Sampaolesi","doi":"10.1007/978-3-030-03095-7_6","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_6","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"126 9 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"121726297","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}