{"title":"Gene Therapy for Central Nervous System in Duchenne Muscular Dystrophy","authors":"C. Vaillend, Faouzi Zarrouki, O. Vacca","doi":"10.1007/978-3-030-03095-7_24","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_24","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"114 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2019-03-31","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"122171496","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
A. Malerba, F. Roth, V. Strings, P. Harish, D. Suhy, C. Trollet, G. Dickson
{"title":"Gene Therapy for Oculopharyngeal Muscular Dystrophy","authors":"A. Malerba, F. Roth, V. Strings, P. Harish, D. Suhy, C. Trollet, G. Dickson","doi":"10.1007/978-3-030-03095-7_31","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_31","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"14 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2017-10-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129907798","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"RNAi Therapy for Dominant Muscular Dystrophies and Other Myopathies","authors":"L. Wallace, Sara E. Garwick, S. Harper","doi":"10.1007/978-1-4419-1207-7_7","DOIUrl":"https://doi.org/10.1007/978-1-4419-1207-7_7","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"125422225","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Animal Models for Muscle Disease and Muscle Gene Therapy","authors":"S. Shrader, Roberta Wrighten, Bruce F. Smith","doi":"10.1007/978-3-030-03095-7_3","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_3","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"9 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"114879517","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Clinical Gene Therapy Trials for Pompe Disease","authors":"C. Liberati, S. Salabarria, M. Corti, B. Byrne","doi":"10.1007/978-3-030-03095-7_44","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_44","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129854568","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Optical Polarization Tractography Imaging of Structural Changes in the Skeletal and Cardiac Muscles of the mdx4cv Mice","authors":"G. Yao","doi":"10.1007/978-3-030-03095-7_13","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_13","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"71 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"125388329","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}