Muscle Gene Therapy最新文献

筛选
英文 中文
Gene Therapy for Central Nervous System in Duchenne Muscular Dystrophy 杜氏肌营养不良患者中枢神经系统的基因治疗
Muscle Gene Therapy Pub Date : 2019-03-31 DOI: 10.1007/978-3-030-03095-7_24
C. Vaillend, Faouzi Zarrouki, O. Vacca
{"title":"Gene Therapy for Central Nervous System in Duchenne Muscular Dystrophy","authors":"C. Vaillend, Faouzi Zarrouki, O. Vacca","doi":"10.1007/978-3-030-03095-7_24","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_24","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"114 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2019-03-31","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"122171496","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 2
Non-viral Vector for Muscle-Mediated Gene Therapy 肌肉介导基因治疗的非病毒载体
Muscle Gene Therapy Pub Date : 2018-12-14 DOI: 10.1007/978-3-030-03095-7_9
S. Braun
{"title":"Non-viral Vector for Muscle-Mediated Gene Therapy","authors":"S. Braun","doi":"10.1007/978-3-030-03095-7_9","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_9","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"16 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2018-12-14","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"114603501","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 3
Gene Therapy for Oculopharyngeal Muscular Dystrophy 眼咽肌萎缩症的基因治疗
Muscle Gene Therapy Pub Date : 2017-10-01 DOI: 10.1007/978-3-030-03095-7_31
A. Malerba, F. Roth, V. Strings, P. Harish, D. Suhy, C. Trollet, G. Dickson
{"title":"Gene Therapy for Oculopharyngeal Muscular Dystrophy","authors":"A. Malerba, F. Roth, V. Strings, P. Harish, D. Suhy, C. Trollet, G. Dickson","doi":"10.1007/978-3-030-03095-7_31","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_31","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"14 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2017-10-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129907798","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 4
RNAi Therapy for Dominant Muscular Dystrophies and Other Myopathies RNAi治疗显性肌营养不良和其他肌病
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-1-4419-1207-7_7
L. Wallace, Sara E. Garwick, S. Harper
{"title":"RNAi Therapy for Dominant Muscular Dystrophies and Other Myopathies","authors":"L. Wallace, Sara E. Garwick, S. Harper","doi":"10.1007/978-1-4419-1207-7_7","DOIUrl":"https://doi.org/10.1007/978-1-4419-1207-7_7","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"125422225","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 4
Molecular Basis of Muscle Disease 肌肉疾病的分子基础
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_2
Ning Liu, R. Bassel-Duby
{"title":"Molecular Basis of Muscle Disease","authors":"Ning Liu, R. Bassel-Duby","doi":"10.1007/978-3-030-03095-7_2","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_2","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"12 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129944720","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Animal Models for Muscle Disease and Muscle Gene Therapy 肌肉疾病动物模型和肌肉基因治疗
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_3
S. Shrader, Roberta Wrighten, Bruce F. Smith
{"title":"Animal Models for Muscle Disease and Muscle Gene Therapy","authors":"S. Shrader, Roberta Wrighten, Bruce F. Smith","doi":"10.1007/978-3-030-03095-7_3","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_3","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"9 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"114879517","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 1
Muscle-Directed Gene Therapy for Alpha-1 Antitrypsin Deficiency α -1抗胰蛋白酶缺乏症的肌肉定向基因治疗
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_45
A. Gruntman, T. Flotte
{"title":"Muscle-Directed Gene Therapy for Alpha-1 Antitrypsin Deficiency","authors":"A. Gruntman, T. Flotte","doi":"10.1007/978-3-030-03095-7_45","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_45","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"33 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"127598596","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 1
Clinical Gene Therapy Trials for Pompe Disease 庞贝病的临床基因治疗试验
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_44
C. Liberati, S. Salabarria, M. Corti, B. Byrne
{"title":"Clinical Gene Therapy Trials for Pompe Disease","authors":"C. Liberati, S. Salabarria, M. Corti, B. Byrne","doi":"10.1007/978-3-030-03095-7_44","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_44","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129854568","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Optical Polarization Tractography Imaging of Structural Changes in the Skeletal and Cardiac Muscles of the mdx4cv Mice mdx4cv小鼠骨骼肌和心肌结构变化的光偏振示踪成像
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_13
G. Yao
{"title":"Optical Polarization Tractography Imaging of Structural Changes in the Skeletal and Cardiac Muscles of the mdx4cv Mice","authors":"G. Yao","doi":"10.1007/978-3-030-03095-7_13","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_13","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"71 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"125388329","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Alternate Translational Initiation of Dystrophin: A Novel Therapeutic Approach 肌营养不良蛋白的交替翻译起始:一种新的治疗方法
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_21
N. Wein, K. Flanigan
{"title":"Alternate Translational Initiation of Dystrophin: A Novel Therapeutic Approach","authors":"N. Wein, K. Flanigan","doi":"10.1007/978-3-030-03095-7_21","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_21","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"14 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"123088221","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
0
×
引用
GB/T 7714-2015
复制
MLA
复制
APA
复制
导出至
BibTeX EndNote RefMan NoteFirst NoteExpress
×
提示
您的信息不完整,为了账户安全,请先补充。
现在去补充
×
提示
您因"违规操作"
具体请查看互助需知
我知道了
×
提示
确定
请完成安全验证×
相关产品
×
本文献相关产品
联系我们:info@booksci.cn Book学术提供免费学术资源搜索服务,方便国内外学者检索中英文文献。致力于提供最便捷和优质的服务体验。 Copyright © 2023 布克学术 All rights reserved.
京ICP备2023020795号-1
ghs 京公网安备 11010802042870号
Book学术文献互助
Book学术文献互助群
群 号:604180095
Book学术官方微信
小红书