Muscle Gene Therapy最新文献

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Preclinical Gene Therapy Studies for Metabolic Myopathy 代谢性肌病的临床前基因治疗研究
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_33
S. Salabarria, B. Byrne, C. Liberati, M. Corti
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引用次数: 0
Gene Therapy for Facioscapulohumeral Muscular Dystrophy (FSHD) 面部肩胛肱肌营养不良症(FSHD)基因治疗
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_29
Daniel G. Miller
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引用次数: 1
Gene Therapy Clinical Trials for Duchenne and Limb Girdle Muscular Dystrophies: Lessons Learned 杜氏肌萎缩症和肢带肌营养不良症的基因治疗临床试验:经验教训
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_41
J. Mendell, L. Rodino-Klapac, C. Walker
{"title":"Gene Therapy Clinical Trials for Duchenne and Limb Girdle Muscular Dystrophies: Lessons Learned","authors":"J. Mendell, L. Rodino-Klapac, C. Walker","doi":"10.1007/978-3-030-03095-7_41","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_41","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"28 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"123297030","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 1
Muscle Cell Membrane Repair and Therapeutic Implications 肌细胞膜修复及其治疗意义
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_26
Renzhi Han
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引用次数: 0
Muscle MRI as an Endpoint in Clinical Trials 肌肉MRI作为临床试验的终点
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_40
D. Fischer, U. Bonati, M. Wattjes
{"title":"Muscle MRI as an Endpoint in Clinical Trials","authors":"D. Fischer, U. Bonati, M. Wattjes","doi":"10.1007/978-3-030-03095-7_40","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_40","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"86 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"123611023","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Considerations on Preclinical Neuromuscular Disease Gene Therapy Studies 临床前神经肌肉疾病基因治疗研究的思考
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_17
D. Duan
{"title":"Considerations on Preclinical Neuromuscular Disease Gene Therapy Studies","authors":"D. Duan","doi":"10.1007/978-3-030-03095-7_17","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_17","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"6 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"121236752","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 5
Gene Replacement Therapy for Duchenne Muscular Dystrophy 杜氏肌营养不良症的基因替代疗法
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_18
K. Hollinger, J. Crudele, J. Chamberlain
{"title":"Gene Replacement Therapy for Duchenne Muscular Dystrophy","authors":"K. Hollinger, J. Crudele, J. Chamberlain","doi":"10.1007/978-3-030-03095-7_18","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_18","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"33 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"121558737","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Muscle Stem Cell Biology and Implications in Gene Therapy 肌肉干细胞生物学及其在基因治疗中的意义
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_4
T. Partridge
{"title":"Muscle Stem Cell Biology and Implications in Gene Therapy","authors":"T. Partridge","doi":"10.1007/978-3-030-03095-7_4","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_4","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"22 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"133560357","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Sarcolipin Knockdown Therapy for Duchenne Muscular Dystrophy 肌肽下调治疗杜氏肌营养不良症
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_23
Satvik Mareedu, S. Dwivedi, N. Niranjan, G. Babu
{"title":"Sarcolipin Knockdown Therapy for Duchenne Muscular Dystrophy","authors":"Satvik Mareedu, S. Dwivedi, N. Niranjan, G. Babu","doi":"10.1007/978-3-030-03095-7_23","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_23","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"381 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"124744933","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 2
Gene Therapy for CMT Inherited Neuropathy CMT遗传性神经病的基因治疗
Muscle Gene Therapy Pub Date : 1900-01-01 DOI: 10.1007/978-3-030-03095-7_35
K. Kleopa, A. Kagiava, I. Sargiannidou
{"title":"Gene Therapy for CMT Inherited Neuropathy","authors":"K. Kleopa, A. Kagiava, I. Sargiannidou","doi":"10.1007/978-3-030-03095-7_35","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_35","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"57 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"125761906","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
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