{"title":"Preclinical Gene Therapy Studies for Metabolic Myopathy","authors":"S. Salabarria, B. Byrne, C. Liberati, M. Corti","doi":"10.1007/978-3-030-03095-7_33","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_33","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"116139967","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Muscle MRI as an Endpoint in Clinical Trials","authors":"D. Fischer, U. Bonati, M. Wattjes","doi":"10.1007/978-3-030-03095-7_40","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_40","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"86 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"123611023","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Sarcolipin Knockdown Therapy for Duchenne Muscular Dystrophy","authors":"Satvik Mareedu, S. Dwivedi, N. Niranjan, G. Babu","doi":"10.1007/978-3-030-03095-7_23","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_23","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"381 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"124744933","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Gene Therapy for CMT Inherited Neuropathy","authors":"K. Kleopa, A. Kagiava, I. Sargiannidou","doi":"10.1007/978-3-030-03095-7_35","DOIUrl":"https://doi.org/10.1007/978-3-030-03095-7_35","url":null,"abstract":"","PeriodicalId":127683,"journal":{"name":"Muscle Gene Therapy","volume":"57 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"125761906","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}