Molecular Therapy: the Journal of the American Society of Gene Therapy最新文献_第2页

Research Highlights. 研究突出了。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-07-08 DOI: 10.1016/j.ymthe.2020.06.019

引用次数: 0

In This Issue. 在本期中。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-06-03 DOI: 10.1016/j.ymthe.2020.05.006

引用次数: 0

Research Highlights. 研究突出了。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-06-03 DOI: 10.1016/j.ymthe.2020.05.008

引用次数: 0

Family Highlights. 家庭的亮点。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-06-01 DOI: 10.1016/j.ymthe.2020.05.009

引用次数: 0

Tryptophanyl-tRNA Synthetase, a Novel Damage-Induced Cytokine, Significantly Increases the Therapeutic Effects of Endometrial Stem Cells. 新型损伤诱导细胞因子色氨酸trna合成酶可显著提高子宫内膜干细胞的治疗效果。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-05-01 DOI: 10.1016/j.jcyt.2020.03.171

Se-Ra Park, Soo-Rim Kim, J. Im, Soyi Lim, I. Hong

引用次数: 5

MicroRNA 223 3p Negatively Regulates the NLRP3 Inflammasome in Acute and Chronic Liver Injury. MicroRNA 223 3p负调控NLRP3炎性体在急慢性肝损伤中的作用

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-02-01 DOI: 10.1016/j.ymthe.2019.09.013

Carolina Jiménez Calvente, Hana Del Pilar, Masahiko Tameda, Casey D. Johnson, A. Feldstein

引用次数: 77

MicroRNA-411 and Its 5'-IsomiR Have Distinct Targets and Functions and Are Differentially Regulated in the Vasculature under Ischemia. MicroRNA-411及其5'-IsomiR具有不同的靶点和功能，在缺血血管中受到不同的调控。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-01-08 Epub Date: 2019-10-07 DOI: 10.1016/j.ymthe.2019.10.002

Reginald V C T van der Kwast, Tamar Woudenberg, Paul H A Quax, A Yaël Nossent

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引用次数: 0

Non-transmissible MV Vector with Segmented RNA Genome Establishes Different Types of iPSCs from Hematopoietic Cells. 利用分段RNA基因组的非传播MV载体从造血细胞中构建不同类型的iPSCs。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-01-01 DOI: 10.1016/j.ymthe.2019.09.007

Takafumi Hiramoto, Maino Tahara, Jiyuan Liao, Y. Soda, Yoshie Miura, R. Kurita, H. Hamana, Kota Inoue, H. Kohara, S. Miyamoto, Y. Hijikata, S. Okano, Y. Yamaguchi, Y. Oda, K. Ichiyanagi, Hidehiro Toh, H. Sasaki, H. Kishi, A. Ryo, A. Muraguchi, M. Takeda, K. Tani

引用次数: 7

Simultaneous Deletion of Endogenous TCRαβ for TCR Gene Therapy Creates an Improved and Safe Cellular Therapeutic. 同时删除内源性TCRαβ用于TCR基因治疗创造了一种改进和安全的细胞治疗方法。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-01-01 DOI: 10.1016/j.ymthe.2019.10.001

Laura T Morton, Rogier M. Reijmers, A. Wouters, C. Kweekel, D. Remst, C. R. Pothast, J. Falkenburg, M. Heemskerk

引用次数: 44

Long-Term Structural Outcomes of Late-Stage RPE65 Gene Therapy. 晚期RPE65基因治疗的长期结构结果。

Molecular Therapy: the Journal of the American Society of Gene Therapy Pub Date : 2020-01-01 DOI: 10.1016/j.ymthe.2019.08.013

Kristin L. Gardiner, A. Cideciyan, M. Świder, V. Dufour, A. Sumaroka, A. Komáromy, W. Hauswirth, S. Iwabe, S. Jacobson, W. Beltran, G. Aguirre

引用次数: 48