晚期RPE65基因治疗的长期结构结果。

{"title":"晚期RPE65基因治疗的长期结构结果。","authors":"Kristin L. Gardiner, A. Cideciyan, M. Świder, V. Dufour, A. Sumaroka, A. Komáromy, W. Hauswirth, S. Iwabe, S. Jacobson, W. Beltran, G. Aguirre","doi":"10.1016/j.ymthe.2019.08.013","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"3 1","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2020-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"48","resultStr":"{\"title\":\"Long-Term Structural Outcomes of Late-Stage RPE65 Gene Therapy.\",\"authors\":\"Kristin L. Gardiner, A. Cideciyan, M. Świder, V. Dufour, A. Sumaroka, A. Komáromy, W. Hauswirth, S. Iwabe, S. Jacobson, W. Beltran, G. Aguirre\",\"doi\":\"10.1016/j.ymthe.2019.08.013\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"\",\"PeriodicalId\":19039,\"journal\":{\"name\":\"Molecular Therapy: the Journal of the American Society of Gene Therapy\",\"volume\":\"3 1\",\"pages\":\"\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2020-01-01\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"48\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"Molecular Therapy: the Journal of the American Society of Gene Therapy\",\"FirstCategoryId\":\"1085\",\"ListUrlMain\":\"https://doi.org/10.1016/j.ymthe.2019.08.013\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"\",\"JCRName\":\"\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Therapy: the Journal of the American Society of Gene Therapy","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymthe.2019.08.013","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}