Sunday, April 23最新文献

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NF1 Recommendation-Based Care Delivery: A Survey of Patients and Caregivers (P3-7.002) NF1基于推荐的护理服务:患者和护理人员的调查(P3-7.002)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000202521
J. Jordan, V. Merker, Lori Chibnik, Yidan Ma, Nicole Ullrich, K. Yohay, P. Knight, Heather B. Radtke, Scott Plotkin
{"title":"NF1 Recommendation-Based Care Delivery: A Survey of Patients and Caregivers (P3-7.002)","authors":"J. Jordan, V. Merker, Lori Chibnik, Yidan Ma, Nicole Ullrich, K. Yohay, P. Knight, Heather B. Radtke, Scott Plotkin","doi":"10.1212/wnl.0000000000202521","DOIUrl":"https://doi.org/10.1212/wnl.0000000000202521","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"9 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"123656080","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Investigation of anxiety, depression, and adjustment disorder in mothers of children with a seizure disorder in the Georgian population (P1-1.011) 格鲁吉亚人群癫痫患儿母亲焦虑、抑郁和适应障碍调查(P1-1.011)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000201940
M. Alavidze, M. Dias, T. Tkemaladze, S. Kasradze
{"title":"Investigation of anxiety, depression, and adjustment disorder in mothers of children with a seizure disorder in the Georgian population (P1-1.011)","authors":"M. Alavidze, M. Dias, T. Tkemaladze, S. Kasradze","doi":"10.1212/wnl.0000000000201940","DOIUrl":"https://doi.org/10.1212/wnl.0000000000201940","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"38 13 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"123673480","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
The Limb Girdle Muscular Dystrophy Health Index (S7.003) 肢带肌营养不良健康指数(S7.003)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000203361
Joy A. Stouffer, K. Bates, Leroy Thacker, C. Heatwole, Nicholas E. Johnson
{"title":"The Limb Girdle Muscular Dystrophy Health Index (S7.003)","authors":"Joy A. Stouffer, K. Bates, Leroy Thacker, C. Heatwole, Nicholas E. Johnson","doi":"10.1212/wnl.0000000000203361","DOIUrl":"https://doi.org/10.1212/wnl.0000000000203361","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"14 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"125750877","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
PGN-EDO51: Preclinical Data Supporting the Development of an Enhanced Delivery Oligonucleotide (EDO) for the Treatment of Duchenne Muscular Dystrophy (DMD) (P3-8.002) pgnn - edo51:临床前数据支持开发增强递送寡核苷酸(EDO)治疗杜氏肌营养不良症(DMD) (p03 -8.002)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000203724
A. Holland, C. Godfrey, P. Lonkar, N. Svenstrup, J. Larkindale, J. McArthur, S. Bracegirdle, J. Goyal
{"title":"PGN-EDO51: Preclinical Data Supporting the Development of an Enhanced Delivery Oligonucleotide (EDO) for the Treatment of Duchenne Muscular Dystrophy (DMD) (P3-8.002)","authors":"A. Holland, C. Godfrey, P. Lonkar, N. Svenstrup, J. Larkindale, J. McArthur, S. Bracegirdle, J. Goyal","doi":"10.1212/wnl.0000000000203724","DOIUrl":"https://doi.org/10.1212/wnl.0000000000203724","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129754880","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Treatment with rhFGF18 Analog Results in Cerebroprotection and Recovery of Motor and Memory Function in a Rat Model of Acute Ischemic Stroke (P3-5.005) rhFGF18类似物对急性缺血性脑卒中大鼠脑保护及运动记忆功能恢复的作用(P3-5.005)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000202207
A. Goraltchouk, Francesco Luppino, A. Seregin
{"title":"Treatment with rhFGF18 Analog Results in Cerebroprotection and Recovery of Motor and Memory Function in a Rat Model of Acute Ischemic Stroke (P3-5.005)","authors":"A. Goraltchouk, Francesco Luppino, A. Seregin","doi":"10.1212/wnl.0000000000202207","DOIUrl":"https://doi.org/10.1212/wnl.0000000000202207","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"43 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129886765","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Centenarians with Cerebrovascular Disease: 38 Patients from a Single Center. How much do we know? What can we improve? (P2-5.021) 患有脑血管疾病的百岁老人:来自同一中心的38例患者我们知道多少?我们可以改进什么?(p2 - 5.021)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000201957
R. Dragomir, Octavio Carranza-Rentería, D. Babici, Lesli Miles-Kiple, K. Kent, D. Barratt
{"title":"Centenarians with Cerebrovascular Disease: 38 Patients from a Single Center. How much do we know? What can we improve? (P2-5.021)","authors":"R. Dragomir, Octavio Carranza-Rentería, D. Babici, Lesli Miles-Kiple, K. Kent, D. Barratt","doi":"10.1212/wnl.0000000000201957","DOIUrl":"https://doi.org/10.1212/wnl.0000000000201957","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"13 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"128527318","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Dose Selection and Clinical Development of Efgartigimod PH20 Subcutaneous in Patients with Generalized Myasthenia Gravis (P1-5.017) Efgartigimod PH20皮下注射治疗广泛性重症肌无力的剂量选择及临床进展(p < 0.01)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000203765
George Li, Yuebing Li, T. Vu, D. Korobko, M. Śmiłowski, Li Liu, Sophie Steeland, B. van Hoorick, J. Podhorná, Jenna Casey, J. Noukens, Tonke van Bragt, K. Utsugisawa, H. Wiendl, J. D. De Bleecker, R. Mantegazza, J. Howard
{"title":"Dose Selection and Clinical Development of Efgartigimod PH20 Subcutaneous in Patients with Generalized Myasthenia Gravis (P1-5.017)","authors":"George Li, Yuebing Li, T. Vu, D. Korobko, M. Śmiłowski, Li Liu, Sophie Steeland, B. van Hoorick, J. Podhorná, Jenna Casey, J. Noukens, Tonke van Bragt, K. Utsugisawa, H. Wiendl, J. D. De Bleecker, R. Mantegazza, J. Howard","doi":"10.1212/wnl.0000000000203765","DOIUrl":"https://doi.org/10.1212/wnl.0000000000203765","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"43 2 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"128224244","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Phenotype and Genotype Heterogeneity of PLA2G6-associated Neurodegeneration (S2.009) pla2g6相关神经变性的表型和基因型异质性(S2.009)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000203574
A. Tavasoli, Ali Zare Dehnavi, Maryam Bemanalizadeh, M. Kahani, M. Rohani, M. B. Toosi, M. Ashrafi, Morteza Heidari, M. Amanat, S. Hosseinpour
{"title":"Phenotype and Genotype Heterogeneity of PLA2G6-associated Neurodegeneration (S2.009)","authors":"A. Tavasoli, Ali Zare Dehnavi, Maryam Bemanalizadeh, M. Kahani, M. Rohani, M. B. Toosi, M. Ashrafi, Morteza Heidari, M. Amanat, S. Hosseinpour","doi":"10.1212/wnl.0000000000203574","DOIUrl":"https://doi.org/10.1212/wnl.0000000000203574","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"128719637","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
A Case of Neural Integrator Failure in Vitamin B1 Deficiency. (P1-9.004) 维生素B1缺乏症中神经整合器功能衰竭1例。(p1 - 9.004)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000203232
Hongying Chen, Niall Warfield, Ciaran Nannery, Z. Togher, Y. Yacoob
{"title":"A Case of Neural Integrator Failure in Vitamin B1 Deficiency. (P1-9.004)","authors":"Hongying Chen, Niall Warfield, Ciaran Nannery, Z. Togher, Y. Yacoob","doi":"10.1212/wnl.0000000000203232","DOIUrl":"https://doi.org/10.1212/wnl.0000000000203232","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"3 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129662798","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Microbiota-derived SCFAs Promote Chronic Neurogenesis and Anti-inflammatory Gene Expression after Traumatic Brain Injury (P1-6.008) 微生物来源的SCFAs促进创伤性脑损伤后慢性神经发生和抗炎基因表达(P1-6.008)
Sunday, April 23 Pub Date : 2023-04-25 DOI: 10.1212/wnl.0000000000203108
Zujian Xiong, Brittany P. Nelson, Chaim T. Sneiderman, Keri L Janesko-Feldman, P. Kochanek, D. Rajasundaram, R. Jha, G. Kohanbash, Dennis Simon
{"title":"Microbiota-derived SCFAs Promote Chronic Neurogenesis and Anti-inflammatory Gene Expression after Traumatic Brain Injury (P1-6.008)","authors":"Zujian Xiong, Brittany P. Nelson, Chaim T. Sneiderman, Keri L Janesko-Feldman, P. Kochanek, D. Rajasundaram, R. Jha, G. Kohanbash, Dennis Simon","doi":"10.1212/wnl.0000000000203108","DOIUrl":"https://doi.org/10.1212/wnl.0000000000203108","url":null,"abstract":"","PeriodicalId":334567,"journal":{"name":"Sunday, April 23","volume":"46 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2023-04-25","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"127061342","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
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