Drug Repurposing最新文献

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Chapter 13. Intellectual Property Considerations 第13章。知识产权考虑
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00264
Hermann Mucke
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引用次数: 0
Chapter 14. Regulatory Considerations and Strategies for Drug Repositioning 第14章。药物重新定位的监管考虑和策略
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00280
K. V. Phelps
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引用次数: 0
Chapter 5. Collaboration Models for Repurposing 第五章。用于重新利用的协作模型
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00074
Bruce Bloom
{"title":"Chapter 5. Collaboration Models for Repurposing","authors":"Bruce Bloom","doi":"10.1039/9781839163401-00074","DOIUrl":"https://doi.org/10.1039/9781839163401-00074","url":null,"abstract":"","PeriodicalId":202024,"journal":{"name":"Drug Repurposing","volume":null,"pages":null},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"127686404","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Chapter 9. Field Discoveries (Case Reports) 第9章。现场发现(病例报告)
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00173
M. Rogosnitzky
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引用次数: 0
Chapter 10. Preclinical. A Repurposed Novel Lyn Kinase Activator, MLR-1023, is a Model Example of Pharmacological Pleiotropy 第十章。临床前。一种重新利用的新型Lyn激酶激活剂MLR-1023是药理多效性的典型例子
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00196
A. Reaume, C. Lipinski
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引用次数: 1
Chapter 11. Harnessing the Potential of Early Access: Advancing Timely Patient Access to Innovative Medicines in a Sustainable Way 第十一章。利用早期获取的潜力:以可持续的方式促进患者及时获得创新药物
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00221
Ingmar de Gooijer, R. Brus
{"title":"Chapter 11. Harnessing the Potential of Early Access: Advancing Timely Patient Access to Innovative Medicines in a Sustainable Way","authors":"Ingmar de Gooijer, R. Brus","doi":"10.1039/9781839163401-00221","DOIUrl":"https://doi.org/10.1039/9781839163401-00221","url":null,"abstract":"The way medicines are developed, regulated and priced determines how quickly patients have access to safe, effective and affordable medicines. Patients are increasingly requesting access to investigational medicines and regulators are developing guidelines for additional data collection outside the clinical trial setting. Payors and healthcare policy makers worry about the rising prices of new medicines and are searching for effective policy instruments. Developing effective pharmaceutical policy requires a thorough understanding of the working of the medicine development ecosystem. Currently the smaller players are the drivers of discovery and innovation but are unable to compete in the approved medicine market as they lack the financial capacity to progress to the commercial phase, which limits competition and pricing pressure. Experimenting with innovative funding models for advanced therapy medicinal products, personalized treatments and medicines targeting (progressive) orphan diseases is expected to occur more frequently. One such model that supports smaller medicine developers, and helps them survive transitioning to the commercial stage, is the funding of early access programs. Countries with universal healthcare systems are well suited to experiment with an adaptive funding model for early access that includes pay-for-performance elements based on evolving real-world data and evaluation. Such an approach has the potential to contribute to universal access to new treatments in a sustainable way.","PeriodicalId":202024,"journal":{"name":"Drug Repurposing","volume":null,"pages":null},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"116738467","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Chapter 3. The Role of Clinical Medicine 第三章。临床医学的作用
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00024
R. Wyse, Antony Cooper, S. Stott
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引用次数: 0
Chapter 2. Role of Academia: Drug Repurposing to Induce Autophagy for Treatment of Neurodegenerative Diseases 第二章。学术界的作用:药物再利用诱导自噬治疗神经退行性疾病
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00014
M. Fernandez-Estévez, L. Wrobel, D. Rubinsztein
{"title":"Chapter 2. Role of Academia: Drug Repurposing to Induce Autophagy for Treatment of Neurodegenerative Diseases","authors":"M. Fernandez-Estévez, L. Wrobel, D. Rubinsztein","doi":"10.1039/9781839163401-00014","DOIUrl":"https://doi.org/10.1039/9781839163401-00014","url":null,"abstract":"","PeriodicalId":202024,"journal":{"name":"Drug Repurposing","volume":null,"pages":null},"PeriodicalIF":0.0,"publicationDate":"1900-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"116547724","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
引用次数: 0
Chapter 7. Cheminformatics Data Mining and Modeling for Drug Repurposing 第七章。药物再利用的化学信息学数据挖掘与建模
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00129
S. Avram, R. Curpan, Tudor I. Oprea
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引用次数: 0
Chapter 4. Role of Industry 第四章。工业的作用
Drug Repurposing Pub Date : 1900-01-01 DOI: 10.1039/9781839163401-00052
D. Hayes, K. Escott
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引用次数: 0
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