{"title":"Antisense Oligonucleotides for Treatment of Neurological Diseases","authors":"R. Seguin","doi":"10.1002/9781119070153.CH15","DOIUrl":"https://doi.org/10.1002/9781119070153.CH15","url":null,"abstract":"","PeriodicalId":405414,"journal":{"name":"Oligonucleotide-Based Drugs and Therapeutics","volume":"20 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2018-06-22","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"129513595","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Hybridization-Dependent Effects","authors":"J. Kitson, P. Kamola, L. Kane","doi":"10.1002/9781119070153.CH7","DOIUrl":"https://doi.org/10.1002/9781119070153.CH7","url":null,"abstract":"","PeriodicalId":405414,"journal":{"name":"Oligonucleotide-Based Drugs and Therapeutics","volume":"10 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2018-06-22","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"121607390","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Reproductive and Developmental Toxicity Testing Strategies for Oligonucleotide-Based Therapeutics","authors":"T. White, J. Cavagnaro","doi":"10.1002/9781119070153.CH11","DOIUrl":"https://doi.org/10.1002/9781119070153.CH11","url":null,"abstract":"","PeriodicalId":405414,"journal":{"name":"Oligonucleotide-Based Drugs and Therapeutics","volume":"13 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2018-06-22","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"133671523","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"CMC Aspects for the Clinical Development of Spiegelmers","authors":"S. Vonhoff","doi":"10.1002/9781119070153.CH18","DOIUrl":"https://doi.org/10.1002/9781119070153.CH18","url":null,"abstract":"","PeriodicalId":405414,"journal":{"name":"Oligonucleotide-Based Drugs and Therapeutics","volume":"116 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2018-06-22","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"115533918","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
K. Brown, M. Puig, L. Haile, D. Ireland, J. Martucci, D. Verthelyi
{"title":"Nucleic Acids as Adjuvants","authors":"K. Brown, M. Puig, L. Haile, D. Ireland, J. Martucci, D. Verthelyi","doi":"10.1002/9781119070153.CH16","DOIUrl":"https://doi.org/10.1002/9781119070153.CH16","url":null,"abstract":"","PeriodicalId":405414,"journal":{"name":"Oligonucleotide-Based Drugs and Therapeutics","volume":"1 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2018-06-22","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"125424846","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Specific Considerations for Preclinical Development of Inhaled Oligonucleotides","authors":"N. Ferrari","doi":"10.1002/9781119070153.CH12","DOIUrl":"https://doi.org/10.1002/9781119070153.CH12","url":null,"abstract":"","PeriodicalId":405414,"journal":{"name":"Oligonucleotide-Based Drugs and Therapeutics","volume":"13 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2018-06-22","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"134296333","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Splice-Switching Oligonucleotides","authors":"I. Gazzoli, A. Aartsma-Rus","doi":"10.1002/9781119070153.CH17","DOIUrl":"https://doi.org/10.1002/9781119070153.CH17","url":null,"abstract":"","PeriodicalId":405414,"journal":{"name":"Oligonucleotide-Based Drugs and Therapeutics","volume":"36 1","pages":"0"},"PeriodicalIF":0.0,"publicationDate":"2018-06-22","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"114341840","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}