{"title":"Methodological challenges in studying disease processes using observational cohort data.","authors":"Richard J Cook, Jerald F Lawless","doi":"10.1007/s42081-024-00276-9","DOIUrl":"10.1007/s42081-024-00276-9","url":null,"abstract":"<p><p>Cohort studies of disease processes deal with events and other outcomes that may occur in individuals following disease onset. The particular goals are often the evaluation of interventions and estimation of the effects of risk factors that may affect the disease course. Models and methods of event history analysis and longitudinal data analysis provide tools for understanding disease processes, but there are numerous challenges in practice. These are related to the complexity of the disease processes and to the difficulty of recruiting representative individuals and acquiring detailed longitudinal data on their disease course. Our objectives here are to describe some of these challenges and to review methods of addressing them. We emphasize the appeal of multistate models as a framework for understanding both disease processes and the processes governing recruitment of individuals for cohort studies and the collection of data. The use of other observational data sources in order to enhance model fitting and analysis is discussed.</p>","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"8 1","pages":"323-345"},"PeriodicalIF":1.1,"publicationDate":"2025-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"https://www.ncbi.nlm.nih.gov/pmc/articles/PMC12179002/pdf/","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144477024","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"OA","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Selection of statistics for a multinomial goodness-of-fit test and a test of independence for a multi-way contingency table when data are sparse","authors":"Nobuhiro Taneichi, Yuri Sekiya","doi":"10.1007/s42081-023-00233-y","DOIUrl":"https://doi.org/10.1007/s42081-023-00233-y","url":null,"abstract":"","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"14 1","pages":"1-32"},"PeriodicalIF":1.3,"publicationDate":"2024-01-03","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"139389613","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Sparse inference of structural equation modeling with latent variables for diffusion processes","authors":"Shogo Kusano, Masayuki Uchida","doi":"10.1007/s42081-023-00230-1","DOIUrl":"https://doi.org/10.1007/s42081-023-00230-1","url":null,"abstract":"","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"3 26","pages":""},"PeriodicalIF":1.3,"publicationDate":"2023-12-26","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"139156637","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Stein-rule M-estimation in sparse partially linear models","authors":"E. Raheem, S. E. Ahmed, Shuangzhe Liu","doi":"10.1007/s42081-023-00231-0","DOIUrl":"https://doi.org/10.1007/s42081-023-00231-0","url":null,"abstract":"","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"132 3","pages":""},"PeriodicalIF":1.3,"publicationDate":"2023-12-23","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"139161078","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Expansion estimators improving the bias and risk of James–Stein’s shrinkage estimator","authors":"Hisayuki Tsukuma","doi":"10.1007/s42081-023-00227-w","DOIUrl":"https://doi.org/10.1007/s42081-023-00227-w","url":null,"abstract":"","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"56 8","pages":""},"PeriodicalIF":1.3,"publicationDate":"2023-12-16","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"138967722","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Bivariate dynamic weighted cumulative residual entropy","authors":"R. Nair, E. I. A. Sathar","doi":"10.1007/s42081-023-00232-z","DOIUrl":"https://doi.org/10.1007/s42081-023-00232-z","url":null,"abstract":"","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"64 2","pages":""},"PeriodicalIF":1.3,"publicationDate":"2023-12-14","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"138974945","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Reliability of stress–strength model for exponentiated Teissier distribution based on lower record values","authors":"Hossein Pasha-Zanoosi","doi":"10.1007/s42081-023-00229-8","DOIUrl":"https://doi.org/10.1007/s42081-023-00229-8","url":null,"abstract":"","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"5 2","pages":""},"PeriodicalIF":1.3,"publicationDate":"2023-12-09","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"138585609","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Shrinkage estimation with logarithmic penalties","authors":"Tatsuya Kubokawa","doi":"10.1007/s42081-023-00225-y","DOIUrl":"https://doi.org/10.1007/s42081-023-00225-y","url":null,"abstract":"","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"11 1","pages":""},"PeriodicalIF":1.3,"publicationDate":"2023-11-29","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"139210453","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Confidence interval for normal means in meta-analysis based on a pretest estimator","authors":"Nanami Taketomi, Yuan-Tsung Chang, Yoshihiko Konno, Mihoko Mori, Takeshi Emura","doi":"10.1007/s42081-023-00221-2","DOIUrl":"https://doi.org/10.1007/s42081-023-00221-2","url":null,"abstract":"","PeriodicalId":29911,"journal":{"name":"Japanese Journal of Statistics and Data Science","volume":"22 1","pages":""},"PeriodicalIF":1.3,"publicationDate":"2023-11-27","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"139233909","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}