{"title":"Call for Papers: MT/MTNA Special Issue on mRNA Therapy.","authors":"R. Frederickson","doi":"10.1016/j.ymthe.2018.05.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2018.05.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"16 1","pages":"1395"},"PeriodicalIF":0.0,"publicationDate":"2018-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"88543501","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Bo Xiao, Zhigang Xu, É. Viennois, Yuchen Zhang, Zhan Zhang, Mingzhen Zhang, Moon K Han, Yuejun Kang, D. Merlin
{"title":"Orally Targeted Delivery of Tripeptide KPV via Hyaluronic Acid-Functionalized Nanoparticles Efficiently Alleviates Ulcerative Colitis.","authors":"Bo Xiao, Zhigang Xu, É. Viennois, Yuchen Zhang, Zhan Zhang, Mingzhen Zhang, Moon K Han, Yuejun Kang, D. Merlin","doi":"10.1016/j.ymthe.2016.11.020","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.020","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"94 1","pages":"1628-1640"},"PeriodicalIF":0.0,"publicationDate":"2017-07-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"90274795","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
T. Lee, J. Yoo, Dan Shu, Hui Li, Jianying Zhang, Jun‐ge Yu, A. C. Jaime-Ramirez, M. Acunzo, G. Romano, R. Cui, Hui-Lung Sun, Zhenghua Luo, M. Old, B. Kaur, Peixuan Guo, C. Croce
{"title":"RNA Nanoparticle-Based Targeted Therapy for Glioblastoma through Inhibition of Oncogenic miR-21.","authors":"T. Lee, J. Yoo, Dan Shu, Hui Li, Jianying Zhang, Jun‐ge Yu, A. C. Jaime-Ramirez, M. Acunzo, G. Romano, R. Cui, Hui-Lung Sun, Zhenghua Luo, M. Old, B. Kaur, Peixuan Guo, C. Croce","doi":"10.1016/j.ymthe.2016.11.016","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.11.016","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"31 1","pages":"1544-1555"},"PeriodicalIF":0.0,"publicationDate":"2017-07-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"80791239","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
M. Weinberg, H. Criswell, S. Powell, A. Bhatt, T. McCown
{"title":"Viral Vector Reprogramming of Adult Resident Striatal Oligodendrocytes into Functional Neurons.","authors":"M. Weinberg, H. Criswell, S. Powell, A. Bhatt, T. McCown","doi":"10.1016/j.ymthe.2017.01.016","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.016","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"12 1","pages":"928-934"},"PeriodicalIF":0.0,"publicationDate":"2017-04-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83465592","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
H. Watkins, C. G. Rappazzo, Jaclyn Higgins, Xiangjie Sun, N. Brock, Annie Chau, Aditya Misra, Joseph P B Cannizzo, M. King, T. Maines, C. Leifer, G. Whittaker, M. DeLisa, D. Putnam
{"title":"Safe Recombinant Outer Membrane Vesicles that Display M2e Elicit Heterologous Influenza Protection.","authors":"H. Watkins, C. G. Rappazzo, Jaclyn Higgins, Xiangjie Sun, N. Brock, Annie Chau, Aditya Misra, Joseph P B Cannizzo, M. King, T. Maines, C. Leifer, G. Whittaker, M. DeLisa, D. Putnam","doi":"10.1016/j.ymthe.2017.01.010","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.010","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"164 1","pages":"989-1002"},"PeriodicalIF":0.0,"publicationDate":"2017-04-05","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"74494865","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"HIV Receives a \"One Two Knockout Punch\".","authors":"C. Cruz, C. Bollard","doi":"10.1016/j.ymthe.2017.02.001","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.02.001","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"44 1","pages":"566-567"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"86554169","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Huifen Zhao, Allistair A. Abraham, Yoon-Sang Kim, Yong-Dong Wang, T. Pestina, J. Zhan, K. Humphries, A. Nienhuis, D. Persons
{"title":"Lentiviral Transfer of γ-Globin with Fusion Gene NUP98-HOXA10HD Expands Hematopoietic Stem Cells and Ameliorates Murine β-Thalassemia.","authors":"Huifen Zhao, Allistair A. Abraham, Yoon-Sang Kim, Yong-Dong Wang, T. Pestina, J. Zhan, K. Humphries, A. Nienhuis, D. Persons","doi":"10.1016/j.ymthe.2017.01.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.01.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"42 1","pages":"593-605"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"91375292","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Genome Editing for Sickle Cell Disease: A Little BCL11A Goes a Long Way.","authors":"Mir A. Hossain, J. Bungert","doi":"10.1016/j.ymthe.2017.02.003","DOIUrl":"https://doi.org/10.1016/j.ymthe.2017.02.003","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"22 1","pages":"561-562"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"73532665","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Hua Wang, Haiyan Zhang, Qiuyi Sun, Yun Wang, Jun Yang, Jincheng Yang, Tao Zhang, S. Luo, Liping Wang, Yu Jiang, C. Zeng, D. Cai, X. Bai
{"title":"Intra-articular Delivery of Antago-miR-483-5p Inhibits Osteoarthritis by Modulating Matrilin 3 and Tissue Inhibitor of Metalloproteinase 2.","authors":"Hua Wang, Haiyan Zhang, Qiuyi Sun, Yun Wang, Jun Yang, Jincheng Yang, Tao Zhang, S. Luo, Liping Wang, Yu Jiang, C. Zeng, D. Cai, X. Bai","doi":"10.1016/j.ymthe.2016.12.020","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.020","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"58 1","pages":"715-727"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"83125130","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
M. Flugelman, M. Halak, B. Yoffe, J. Schneiderman, Chen Rubinstein, A. Bloom, E. Weinmann, I. Goldin, V. Ginzburg, O. Mayzler, A. Hoffman, B. Koren, D. Gershtein, M. Inbar, Marina Hutoran, Adili Tsaba
{"title":"Phase Ib Safety, Two-Dose Study of MultiGeneAngio in Patients with Chronic Critical Limb Ischemia.","authors":"M. Flugelman, M. Halak, B. Yoffe, J. Schneiderman, Chen Rubinstein, A. Bloom, E. Weinmann, I. Goldin, V. Ginzburg, O. Mayzler, A. Hoffman, B. Koren, D. Gershtein, M. Inbar, Marina Hutoran, Adili Tsaba","doi":"10.1016/j.ymthe.2016.12.019","DOIUrl":"https://doi.org/10.1016/j.ymthe.2016.12.019","url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"14 1","pages":"816-825"},"PeriodicalIF":0.0,"publicationDate":"2017-03-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"91145909","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":0,"RegionCategory":"","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}