Harsh Parikh, Rachael K Ross, Elizabeth Stuart, Kara E Rudolph
{"title":"<i>Who Are We Missing?</i>: A Principled Approach to Characterizing the Underrepresented Population.","authors":"Harsh Parikh, Rachael K Ross, Elizabeth Stuart, Kara E Rudolph","doi":"10.1080/01621459.2025.2495319","DOIUrl":"10.1080/01621459.2025.2495319","url":null,"abstract":"<p><p>Randomized controlled trials (RCTs) serve as the cornerstone for understanding causal effects, yet extending inferences to target populations presents challenges due to effect heterogeneity and underrepresentation. Our paper addresses the critical issue of identifying and characterizing underrepresented subgroups in RCTs, proposing a novel framework for refining target populations to improve generalizability. We introduce an optimization-based approach, Rashomon Set of Optimal Trees (ROOT), to characterize underrepresented groups. ROOT optimizes the target subpopulation distribution by minimizing the variance of the target average treatment effect estimate, ensuring more precise treatment effect estimations. Notably, ROOT generates interpretable characteristics of the underrepresented population, aiding researchers in effective communication. Our approach demonstrates improved precision and interpretability compared to alternatives, as illustrated with synthetic data experiments. We apply our methodology to extend inferences from the Starting Treatment with Agonist Replacement Therapies (START) trial - investigating the effectiveness of medication for opioid use disorder - to the real-world population represented by the Treatment Episode Dataset: Admissions (TEDS-A). By refining target populations using ROOT, our framework offers a systematic approach to enhance decision-making accuracy and inform future trials in diverse populations.</p>","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":" ","pages":""},"PeriodicalIF":3.0,"publicationDate":"2025-06-24","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"https://www.ncbi.nlm.nih.gov/pmc/articles/PMC12393784/pdf/","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144958722","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"OA","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"A practical interval estimation method for spectral density function","authors":"Haihan Yu, Mark S. Kaiser, Daniel J. Nordman","doi":"10.1080/01621459.2025.2516211","DOIUrl":"https://doi.org/10.1080/01621459.2025.2516211","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"15 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-18","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144319773","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Communication-Efficient Distributed Estimation and Inference for Cox’s Model","authors":"Pierre Bayle, Jianqing Fan, Zhipeng Lou","doi":"10.1080/01621459.2025.2516820","DOIUrl":"https://doi.org/10.1080/01621459.2025.2516820","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"29 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-18","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144320037","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Testing Elliptical Models in High Dimensions","authors":"Siyao Wang, Miles E. Lopes","doi":"10.1080/01621459.2025.2518617","DOIUrl":"https://doi.org/10.1080/01621459.2025.2518617","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"82 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-18","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144320038","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Design-Based Causal Inference with Missing Outcomes: Missingness Mechanisms, Imputation-Assisted Randomization Tests, and Covariate Adjustment","authors":"Siyu Heng, Jiawei Zhang, Yang Feng","doi":"10.1080/01621459.2025.2516204","DOIUrl":"https://doi.org/10.1080/01621459.2025.2516204","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"5 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-18","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144319775","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Mutually exciting point processes with latency*","authors":"Yoann Potiron, Vladimir Volkov","doi":"10.1080/01621459.2025.2516209","DOIUrl":"https://doi.org/10.1080/01621459.2025.2516209","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"42 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-12","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144278218","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
František Bartoš, Alexandra Sarafoglou, Henrik R. Godmann, Amir Sahrani, David Klein Leunk, Pierre Y. Gui, David Voss, Kaleem Ullah, Malte J. Zoubek, Franziska Nippold, Frederik Aust, Felipe F. Vieira, Chris-Gabriel Islam, Anton J. Zoubek, Sara Shabani, Jonas Petter, Ingeborg B. Roos, Adam Finnemann, Aaron B. Lob, Madlen F. Hoffstadt, Jason Nak, Jill de Ron, Koen Derks, Karoline Huth, Sjoerd Terpstra, Thomas Bastelica, Magda Matetovici, Vincent L. Ott, Andreea S. Zetea, Katharina Karnbach, Michelle C. Donzallaz, Arne John, Roy M. Moore, Franziska Assion, Riet van Bork, Theresa E. Leidinger, Xiaochang Zhao, Adrian Karami Motaghi, Ting Pan, Hannah Armstrong, Tianqi Peng, Mara Bialas, Joyce Y.-C. Pang, Bohan Fu, Shujun Yang, Xiaoyi Lin, Dana Sleiffer, Miklos Bognar, Balazs Aczel, Eric-Jan Wagenmakers
{"title":"Fair Coins Tend to Land on the Same Side They Started: Evidence from 350,757 Flips","authors":"František Bartoš, Alexandra Sarafoglou, Henrik R. Godmann, Amir Sahrani, David Klein Leunk, Pierre Y. Gui, David Voss, Kaleem Ullah, Malte J. Zoubek, Franziska Nippold, Frederik Aust, Felipe F. Vieira, Chris-Gabriel Islam, Anton J. Zoubek, Sara Shabani, Jonas Petter, Ingeborg B. Roos, Adam Finnemann, Aaron B. Lob, Madlen F. Hoffstadt, Jason Nak, Jill de Ron, Koen Derks, Karoline Huth, Sjoerd Terpstra, Thomas Bastelica, Magda Matetovici, Vincent L. Ott, Andreea S. Zetea, Katharina Karnbach, Michelle C. Donzallaz, Arne John, Roy M. Moore, Franziska Assion, Riet van Bork, Theresa E. Leidinger, Xiaochang Zhao, Adrian Karami Motaghi, Ting Pan, Hannah Armstrong, Tianqi Peng, Mara Bialas, Joyce Y.-C. Pang, Bohan Fu, Shujun Yang, Xiaoyi Lin, Dana Sleiffer, Miklos Bognar, Balazs Aczel, Eric-Jan Wagenmakers","doi":"10.1080/01621459.2025.2516210","DOIUrl":"https://doi.org/10.1080/01621459.2025.2516210","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"1 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-12","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144278215","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Incorporating Auxiliary Variables to Improve the Efficiency of Time-Varying Treatment Effect Estimation","authors":"Jieru Shi, Zhenke Wu, Walter Dempsey","doi":"10.1080/01621459.2025.2516197","DOIUrl":"https://doi.org/10.1080/01621459.2025.2516197","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"25 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-12","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144278219","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
Nicole Augustin, Axel Albrecht, Karim Anaya-Izquierdo, Alice Davis, Stefan Meining, Heike Puhlmann, Simon Wood
{"title":"Modelling tree survival for investigating climate change effects","authors":"Nicole Augustin, Axel Albrecht, Karim Anaya-Izquierdo, Alice Davis, Stefan Meining, Heike Puhlmann, Simon Wood","doi":"10.1080/01621459.2025.2516181","DOIUrl":"https://doi.org/10.1080/01621459.2025.2516181","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"7 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-12","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144278223","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}
{"title":"Conformal Prediction for Network-Assisted Regression","authors":"Robert Lunde, Elizaveta Levina, Ji Zhu","doi":"10.1080/01621459.2025.2506198","DOIUrl":"https://doi.org/10.1080/01621459.2025.2506198","url":null,"abstract":"","PeriodicalId":17227,"journal":{"name":"Journal of the American Statistical Association","volume":"37 1","pages":""},"PeriodicalIF":3.7,"publicationDate":"2025-06-10","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":null,"resultStr":null,"platform":"Semanticscholar","paperid":"144260003","PeriodicalName":null,"FirstCategoryId":null,"ListUrlMain":null,"RegionNum":1,"RegionCategory":"数学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":"","EPubDate":null,"PubModel":null,"JCR":null,"JCRName":null,"Score":null,"Total":0}