包裹性地塞米松磷酸钠对6-9岁儿童共济失调毛细血管扩张症(NEAT)的神经系统影响:一项多中心、随机、双盲、安慰剂对照的3期试验

Sam Russo, Stefan Zielen, Barbara Pietrucha, Jordis Trischler, Susan Perlman, Daniel Zielonka, Maria del Mar Garcia Romero, Winnie Ip, Asbjørg Stray-Pedersen, Malene Landbo Børresen, David Gomez-Andres, Samantha Lissauer, Jana Pachlopnik-Schmid, Konstantinos Karampatsas, Steve Wu, Francesco Pisani, Howard Lederman, Raffaele Badolato, Jan Kern, Oliver Kornmann, Helena Donath, William P Whitehouse, Mary Kay Koenig, Hassan Abolhassani, Caralee Schaefer, Maureen Roden, Dirk Thye, Alex Smith, Biljana Horn, Andrew Prayle
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Neurological effects of encapsulated dexamethasone sodium phosphate in children aged 6–9 years with ataxia telangiectasia (NEAT): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
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