Sam Russo, Stefan Zielen, Barbara Pietrucha, Jordis Trischler, Susan Perlman, Daniel Zielonka, Maria del Mar Garcia Romero, Winnie Ip, Asbjørg Stray-Pedersen, Malene Landbo Børresen, David Gomez-Andres, Samantha Lissauer, Jana Pachlopnik-Schmid, Konstantinos Karampatsas, Steve Wu, Francesco Pisani, Howard Lederman, Raffaele Badolato, Jan Kern, Oliver Kornmann, Helena Donath, William P Whitehouse, Mary Kay Koenig, Hassan Abolhassani, Caralee Schaefer, Maureen Roden, Dirk Thye, Alex Smith, Biljana Horn, Andrew Prayle
{"title":"包裹性地塞米松磷酸钠对6-9岁儿童共济失调毛细血管扩张症(NEAT)的神经系统影响:一项多中心、随机、双盲、安慰剂对照的3期试验","authors":"Sam Russo, Stefan Zielen, Barbara Pietrucha, Jordis Trischler, Susan Perlman, Daniel Zielonka, Maria del Mar Garcia Romero, Winnie Ip, Asbjørg Stray-Pedersen, Malene Landbo Børresen, David Gomez-Andres, Samantha Lissauer, Jana Pachlopnik-Schmid, Konstantinos Karampatsas, Steve Wu, Francesco Pisani, Howard Lederman, Raffaele Badolato, Jan Kern, Oliver Kornmann, Helena Donath, William P Whitehouse, Mary Kay Koenig, Hassan Abolhassani, Caralee Schaefer, Maureen Roden, Dirk Thye, Alex Smith, Biljana Horn, Andrew Prayle","doi":"10.1016/s2352-4642(26)00125-2","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":94246,"journal":{"name":"The Lancet. Child & adolescent health","volume":"34 1","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2026-08-14","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"Neurological effects of encapsulated dexamethasone sodium phosphate in children aged 6–9 years with ataxia telangiectasia (NEAT): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial\",\"authors\":\"Sam Russo, Stefan Zielen, Barbara Pietrucha, Jordis Trischler, Susan Perlman, Daniel Zielonka, Maria del Mar Garcia Romero, Winnie Ip, Asbjørg Stray-Pedersen, Malene Landbo Børresen, David Gomez-Andres, Samantha Lissauer, Jana Pachlopnik-Schmid, Konstantinos Karampatsas, Steve Wu, Francesco Pisani, Howard Lederman, Raffaele Badolato, Jan Kern, Oliver Kornmann, Helena Donath, William P Whitehouse, Mary Kay Koenig, Hassan Abolhassani, Caralee Schaefer, Maureen Roden, Dirk Thye, Alex Smith, Biljana Horn, Andrew Prayle\",\"doi\":\"10.1016/s2352-4642(26)00125-2\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"\",\"PeriodicalId\":94246,\"journal\":{\"name\":\"The Lancet. Child & adolescent health\",\"volume\":\"34 1\",\"pages\":\"\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2026-08-14\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"The Lancet. Child & adolescent health\",\"FirstCategoryId\":\"0\",\"ListUrlMain\":\"https://doi.org/10.1016/s2352-4642(26)00125-2\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"\",\"JCRName\":\"\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"The Lancet. Child & adolescent health","FirstCategoryId":"0","ListUrlMain":"https://doi.org/10.1016/s2352-4642(26)00125-2","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}
Neurological effects of encapsulated dexamethasone sodium phosphate in children aged 6–9 years with ataxia telangiectasia (NEAT): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial