通过USNPMSC Registry评估儿童多发性硬化症患者使用Avonex或Plegridy的疗效结局。

IF 1.6 4区 医学 Q3 CLINICAL NEUROLOGY
Melissa A Wright, Bradley J Barney, Skyler Peterson, Michael Waltz, John Rose, Mary Rensel, Aaron Abrams, Emmanuelle Waubant, Yolanda Wheeler, Moses Rodriguez, Jan-Mendelt Tillema, Lauren Krupp, Mark Gorman, Leslie Benson, Timothy Lotze, Nikita Shukla, Soe Mar, Tanuja Chitnis, Teri Schreiner, Megan Vignos, T Charles Casper
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引用次数: 0

摘要

本研究利用美国儿童多发性硬化症中心网络的数据,评估了多发性硬化症疾病改善疗法,肌肉注射干扰素β -1a (Avonex)和皮下聚乙二醇干扰素β -1a (Plegridy)的疗效。在这项回顾性分析中,纳入了154例多发性硬化症患者,他们在18岁之前接受了Avonex (n = 130)、Plegridy (n = 23)或两种治疗(n = 1)。经过3个月的持续适应期(“入期”),avonex治疗的患者第一年无复发的概率为68.3%,plegridy治疗的患者为69.9%;年复发率分别为0.50和0.59。两种疾病改善疗法的疗效与在成人人群中报道的相似。尽管缺乏正式批准用于儿童多发性硬化症,但这些结果表明,患者可能从Avonex或Plegridy治疗中获益。了解儿童多发性硬化症特定疾病改善疗法的疗效对于做出明智的治疗决定至关重要。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Evaluating Efficacy Outcomes in Pediatric Multiple Sclerosis Patients While Using Avonex or Plegridy via USNPMSC Registry.

This study evaluated the efficacy of the multiple sclerosis disease-modifying therapies, intramuscular interferon beta-1a (Avonex) and subcutaneous peginterferon beta-1a (Plegridy), using data from the United States Network of Pediatric Multiple Sclerosis Centers. In this retrospective analysis, 154 patients with multiple sclerosis were included who were treated with Avonex (n = 130), Plegridy (n = 23), or both treatments (n = 1) before the age of 18 years. After 3 months' sustained use acclimation ("wash-in"), the probability of being relapse-free during the first year was 68.3% for Avonex-treated patients and 69.9% for Plegridy-treated patients; annualized relapse rates were 0.50 and 0.59, respectively. Both disease-modifying therapies demonstrated efficacy similar to that reported in adult populations. Despite the lack of formal approval for pediatric multiple sclerosis, these outcomes indicate that patients may benefit from treatment with Avonex or Plegridy. Understanding efficacy of specific disease-modifying therapies in pediatric multiple sclerosis is essential to making informed treatment decisions.

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来源期刊
Journal of Child Neurology
Journal of Child Neurology 医学-临床神经学
CiteScore
4.20
自引率
5.30%
发文量
111
审稿时长
3-6 weeks
期刊介绍: The Journal of Child Neurology (JCN) embraces peer-reviewed clinical and investigative studies from a wide-variety of neuroscience disciplines. Focusing on the needs of neurologic patients from birth to age 18 years, JCN covers topics ranging from assessment of new and changing therapies and procedures; diagnosis, evaluation, and management of neurologic, neuropsychiatric, and neurodevelopmental disorders; and pathophysiology of central nervous system diseases.
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