神经发育障碍患者的长读测序揭示了涉及ARID1B基因的复杂重排。

IF 1.7 4区 生物学 Q3 GENETICS & HEREDITY
Tam P Sneddon, Scott A Melville, Mai Xiong, Kimberly Foss, Emma B Cardwell, Kelly Rafferty, Karen E Weck, Ana Berglind, Erin L Heinzen, Matt L Tedder, Muge Gucsavas-Calikoglu, Yael Shiloh-Malawsky, Zheng Jane Fan, Bradford C Powell, Senyene E Hunter
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引用次数: 0

摘要

长读段测序可以识别短读段测序无法识别的致病变异。在这里,我们报告了使用牛津纳米孔技术长读测序来解决涉及ARID1B基因的复杂易位反转,该患者为一名5岁男性,有发热性癫痫发作、顽固性癫痫、癫痫性脑病和语言迟缓的病史。先前的临床基因检测包括核型t(6;11)(q25.3;q22.3)明显平衡易位,染色体微阵列在4p13中有1.48 Mb间质缺失,两者都被认为没有临床意义,正常的脆性X和prder - willi /Angelman DNA检测,癫痫或神经递质疾病基因面板没有明显发现。广泛的代谢测试也呈阴性。该患者被纳入北卡罗来纳大学(UNC)神经和发育障碍遗传决定因素(GDNDD)研究。研究短读基因组单核苷酸和结构变异分析均为阴性。随后通过长读测序发现,该易位中断了ARID1B基因,这突出了长读测序在识别和解决遗传疾病潜在的复杂重排方面的应用,并可能在确定其他遗传疾病的不明原因的平衡易位的致病性方面具有价值。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Long-Read Sequencing of a Neurodevelopmental Disorder Patient Reveals Complex Rearrangement Involving the ARID1B Gene.

Long-read sequencing can identify disease-causing variants that are missed by short-read sequencing. Here, we report the use of Oxford Nanopore Technology long-read sequencing to resolve a complex translocation-inversion involving the ARID1B gene in a 5-year-old male with a history of febrile seizures, intractable epilepsy, epileptic encephalopathy, and speech delay. Prior clinical genetic testing included a karyotype with a t(6;11)(q25.3;q22.3) apparently balanced translocation and a chromosomal microarray with a 1.48 Mb interstitial deletion within 4p13 that were both deemed not clinically significant, normal fragile X and Prader-Willi/Angelman DNA assays, and no significant findings on epilepsy or neurotransmitter disorders gene panels. Extensive metabolic testing was also negative. The patient was enrolled in the University of North Carolina (UNC) Genetic Determinants of Neurological and Developmental Disorders (GDNDD) study. Research short-read genome single nucleotide and structural variant analysis was negative. Subsequent identification by long-read sequencing that the translocation interrupted the ARID1B gene highlights the use of long-read sequencing to identify and resolve complex rearrangements underlying genetic disorders and may be valuable in determining the pathogenicity of unexplained balanced translocations for other genetic disorders.

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来源期刊
CiteScore
3.50
自引率
5.00%
发文量
432
审稿时长
2-4 weeks
期刊介绍: The American Journal of Medical Genetics - Part A (AJMG) gives you continuous coverage of all biological and medical aspects of genetic disorders and birth defects, as well as in-depth documentation of phenotype analysis within the current context of genotype/phenotype correlations. In addition to Part A , AJMG also publishes two other parts: Part B: Neuropsychiatric Genetics , covering experimental and clinical investigations of the genetic mechanisms underlying neurologic and psychiatric disorders. Part C: Seminars in Medical Genetics , guest-edited collections of thematic reviews of topical interest to the readership of AJMG .
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