贝叶斯方法对潜在亚群的识别。

IF 1.9 3区 医学 Q3 HEALTH CARE SCIENCES & SERVICES
Ethan M Alt, Peter Yi Guan, Larry Leon, Amarjot Kaur, Yue Shentu, Guoqing Diao, Xianming Tan, Joseph G Ibrahim
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引用次数: 0

摘要

在临床试验中,人们常常想知道治疗对某些群体的效果是否不同,这被称为治疗效果的异质性。这样的亚组分析进行起来很复杂,因为试验通常无法找到亚组。此外,很难确定属于这些亚组的患者的特征。在本文中,我们提出了一个半参数混合模型来识别具有时间到事件结果的子群。具体来说,我们假设了一个具有亚组特异性分段恒定基线风险的比例风险模型,其中亚组特异性治疗效果假设在每个子组中是相同的。属于某一亚群的概率是患者预后因素的函数。采用贝叶斯方法,考虑了分类不确定性。我们通过模拟和应用于HIV研究中真实临床试验的数据来证明我们的方法的实用性。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
A Bayesian approach towards the identification of latent subgroups.

In clinical trials, it is often of interest to know whether treatment works differently for some groups than others, known as heterogeneity of treatment effect. Such subgroup analysis is complicated to conduct because trials are typically not powered to find subgroups. Furthermore, it is difficult to identify characteristics of patients pertaining to such subgroups. In this article, we propose a semiparametric mixture model to identify subgroups with time-to-event outcomes. Specifically, we assume a proportional hazards model with subgroup-specific piecewise constant baseline hazards, where the subgroup-specific treatment effect is assumed to be the same within each subgroup. The probability of belonging to a certain subgroup is a function of patient prognostic factors. Adopting a Bayesian approach, classification uncertainty is taken into account. We demonstrate the utility of our approach via simulation and an application to data from a real clinical trial in HIV research.

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来源期刊
Statistical Methods in Medical Research
Statistical Methods in Medical Research 医学-数学与计算生物学
CiteScore
4.10
自引率
4.30%
发文量
127
审稿时长
>12 weeks
期刊介绍: Statistical Methods in Medical Research is a peer reviewed scholarly journal and is the leading vehicle for articles in all the main areas of medical statistics and an essential reference for all medical statisticians. This unique journal is devoted solely to statistics and medicine and aims to keep professionals abreast of the many powerful statistical techniques now available to the medical profession. This journal is a member of the Committee on Publication Ethics (COPE)
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