监管机构能否在促进帕金森病新药开发方面发挥作用?

IF 5 3区 医学 Q2 NEUROSCIENCES
Mário Miguel Rosa, Ewa Balkowiec-Iskra
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引用次数: 0

摘要

帕金森病(PD)是第二常见的神经退行性疾病,其患病率在过去25年中翻了一番。左旋多巴的新配方最近已经上市,提高了治疗PD的能力,但在欧盟,自2015年以来没有新的PD活性物质上市,而两种新药已在其他地方上市。尽管帕金森病是最可治疗的神经退行性疾病,但仍存在一些未满足的医疗需求,需要研究人员、药物开发商和监管机构共同努力,以促进该领域的进一步发展。有几个原因可以解释PD缺乏新的治疗方法。监管机构提供科学建议,并制定了几个促进药物开发的项目。本文讨论了在开发过程中发现的主要障碍,欧盟和美国批准的现状,以及目前优化药物开发和营销的可用机制。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Can regulators have a role in facilitating the development of new medicines for Parkinson's disease?

Parkinson's disease (PD) is the second most frequent neurodegenerative disorder, and its prevalence has doubled in the past 25 years. New formulations of levodopa have recently been marketed that improved the ability to treat PD, but in the European Union, no new active substance for PD has been marketed since 2015, whilst two new agents have been marketed elsewhere. In spite of being the most treatable neurodegenerative disorder, several unmet medical needs still exists in PD, and efforts both from researchers, drug developers and regulators are needed to facilitate further developments in the field. There are several reasons that may account for the lack of new treatments for PD. Regulatory agencies provide scientific advice and have developed several programs to foster drug development. This manuscript discusses the main obstacles identified in the development process, the present status of approvals in European Union and the United States, and the presently available mechanisms to optimize drug development and marketing.

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来源期刊
CiteScore
8.40
自引率
5.80%
发文量
338
审稿时长
>12 weeks
期刊介绍: The Journal of Parkinson''s Disease (JPD) publishes original research in basic science, translational research and clinical medicine in Parkinson’s disease in cooperation with the Journal of Alzheimer''s Disease. It features a first class Editorial Board and provides rigorous peer review and rapid online publication.
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