{"title":"严重间质性肺疾病是家族病例中STING1变异的首次表现。","authors":"Zhijuan Kang, Ruqian Fu, Zhihui Li, Liang Zhang","doi":"10.1007/s12026-025-09670-1","DOIUrl":null,"url":null,"abstract":"<p><p>STING-associated vasculopathy with onset in infancy (SAVI) is a very rare autosomal-dominant Mendelian autoinflammatory disease caused by heterozygous gain-of-function mutations in STING1. Reported carriers of a STING1 gain-of-function mutations are mostly symptomatic. Herein, we present a case study of an infant who presented with cyanosis, dyspnea, clubbing fingers, failure to thrive, and widespread interstitial changes, all consistent with interstitial lung disease (ILD); however, there was a notable lack of characteristic cutaneous features and recurrent fever. Whole-exome sequencing detected a pathogenic heterozygous mutation (p.Arg218Gln) in STING1. Intriguingly, this mutation was also present in her father (aged 32 years), whereas this carrier was healthy and without clinical symptoms. This study emphasizes the need to consider the possibility of SAVI in infants with ILD, even if they lack typical manifestations. Our study also underlines the possibility that carriers with STING gain-of-function mutations are clinically asymptomatic.</p>","PeriodicalId":13389,"journal":{"name":"Immunologic Research","volume":"73 1","pages":"113"},"PeriodicalIF":3.1000,"publicationDate":"2025-07-29","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"Severe interstitial lung disease as the first manifestation of a STING1 variant in a familial case.\",\"authors\":\"Zhijuan Kang, Ruqian Fu, Zhihui Li, Liang Zhang\",\"doi\":\"10.1007/s12026-025-09670-1\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"<p><p>STING-associated vasculopathy with onset in infancy (SAVI) is a very rare autosomal-dominant Mendelian autoinflammatory disease caused by heterozygous gain-of-function mutations in STING1. Reported carriers of a STING1 gain-of-function mutations are mostly symptomatic. Herein, we present a case study of an infant who presented with cyanosis, dyspnea, clubbing fingers, failure to thrive, and widespread interstitial changes, all consistent with interstitial lung disease (ILD); however, there was a notable lack of characteristic cutaneous features and recurrent fever. Whole-exome sequencing detected a pathogenic heterozygous mutation (p.Arg218Gln) in STING1. Intriguingly, this mutation was also present in her father (aged 32 years), whereas this carrier was healthy and without clinical symptoms. This study emphasizes the need to consider the possibility of SAVI in infants with ILD, even if they lack typical manifestations. Our study also underlines the possibility that carriers with STING gain-of-function mutations are clinically asymptomatic.</p>\",\"PeriodicalId\":13389,\"journal\":{\"name\":\"Immunologic Research\",\"volume\":\"73 1\",\"pages\":\"113\"},\"PeriodicalIF\":3.1000,\"publicationDate\":\"2025-07-29\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"Immunologic Research\",\"FirstCategoryId\":\"3\",\"ListUrlMain\":\"https://doi.org/10.1007/s12026-025-09670-1\",\"RegionNum\":4,\"RegionCategory\":\"医学\",\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"Q3\",\"JCRName\":\"IMMUNOLOGY\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"Immunologic Research","FirstCategoryId":"3","ListUrlMain":"https://doi.org/10.1007/s12026-025-09670-1","RegionNum":4,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"Q3","JCRName":"IMMUNOLOGY","Score":null,"Total":0}
Severe interstitial lung disease as the first manifestation of a STING1 variant in a familial case.
STING-associated vasculopathy with onset in infancy (SAVI) is a very rare autosomal-dominant Mendelian autoinflammatory disease caused by heterozygous gain-of-function mutations in STING1. Reported carriers of a STING1 gain-of-function mutations are mostly symptomatic. Herein, we present a case study of an infant who presented with cyanosis, dyspnea, clubbing fingers, failure to thrive, and widespread interstitial changes, all consistent with interstitial lung disease (ILD); however, there was a notable lack of characteristic cutaneous features and recurrent fever. Whole-exome sequencing detected a pathogenic heterozygous mutation (p.Arg218Gln) in STING1. Intriguingly, this mutation was also present in her father (aged 32 years), whereas this carrier was healthy and without clinical symptoms. This study emphasizes the need to consider the possibility of SAVI in infants with ILD, even if they lack typical manifestations. Our study also underlines the possibility that carriers with STING gain-of-function mutations are clinically asymptomatic.
期刊介绍:
IMMUNOLOGIC RESEARCH represents a unique medium for the presentation, interpretation, and clarification of complex scientific data. Information is presented in the form of interpretive synthesis reviews, original research articles, symposia, editorials, and theoretical essays. The scope of coverage extends to cellular immunology, immunogenetics, molecular and structural immunology, immunoregulation and autoimmunity, immunopathology, tumor immunology, host defense and microbial immunity, including viral immunology, immunohematology, mucosal immunity, complement, transplantation immunology, clinical immunology, neuroimmunology, immunoendocrinology, immunotoxicology, translational immunology, and history of immunology.