一种强大的机器学习方法预测bDMARDs治疗的类风湿关节炎患者的缓解和分层风险。

IF 3.9 2区 综合性期刊 Q1 MULTIDISCIPLINARY SCIENCES
Fatemeh Salehi, Emmanuelle Salin, Benjamin Smarr, Sara Bayat, Arnd Kleyer, Georg Schett, Ruth Fritsch-Stork, Bjoern M Eskofier
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引用次数: 0

摘要

类风湿性关节炎(RA)是一种慢性自身免疫性疾病,影响全球数百万人,导致炎症、关节损伤和生活质量下降。虽然生物疾病缓解抗风湿药物(bDMARDs)是有效的,但它们是昂贵的,并且高达40%的患者不能在6个月内达到缓解。准确预测治疗反应对于优化护理、减少副作用和提高成本效益至关重要。本研究提出了一个强大的机器学习框架,用于使用基线常规临床数据预测RA患者6个月的缓解。该框架还整合了风险分层和可解释性,以增强其临床适用性。我们评估了多个机器学习模型,AdaBoost, Random Forest, XGBoost和支持向量机,使用来自奥地利RA患者的数据。我们在埃尔兰根医院的独立数据集上对结果进行了外部验证。为了提高可操作风险分层概率估计的可靠性,我们采用了校准技术,包括Platt标度、等压回归、Beta校准和样条校准。我们生成校准曲线来评估和可视化预测概率与观察结果之间的一致性。此外,我们使用SHapley加性解释(SHAP)来分析不同患者特征对RA缓解预测的贡献。AdaBoost在等渗回归标定下的准确率为85.71%,Brier评分为0.13。SHAP确定DAS28、视觉模拟量表(VAS)、年龄和肿胀关节计数(SJC)是预测RA缓解的重要特征。我们还根据模型预测将患者分为低、中、高风险三类,以支持随访计划和治疗优先级。我们的框架预测在bDMARD治疗开始前RA缓解。它可以实现个性化护理、可操作的风险分层和优化的资源分配。在两个不同的个体队列数据集上验证了其稳健性,这突出了其整合到常规临床工作流程中的潜力。
本文章由计算机程序翻译,如有差异,请以英文原文为准。

A robust machine learning approach to predicting remission and stratifying risk in rheumatoid arthritis patients treated with bDMARDs.

A robust machine learning approach to predicting remission and stratifying risk in rheumatoid arthritis patients treated with bDMARDs.

A robust machine learning approach to predicting remission and stratifying risk in rheumatoid arthritis patients treated with bDMARDs.

A robust machine learning approach to predicting remission and stratifying risk in rheumatoid arthritis patients treated with bDMARDs.

Rheumatoid arthritis (RA) is a chronic autoimmune disease affecting millions worldwide, leading to inflammation, joint damage, and reduced quality of life. Although biological disease-modifying antirheumatic drugs (bDMARDs) are effective, they are costly, and up to 40% of patients do not achieve remission within six months. Accurate prediction of treatment response is crucial for optimizing care, minimizing side effects, and enhancing cost efficiency. This study proposes a robust machine learning framework for predicting six-month remission in RA patients using baseline routine clinical data. The framework also integrates risk stratification and explainability to enhance its clinical applicability. We evaluated multiple machine learning models, AdaBoost, Random Forest, XGBoost, and Support Vector Machines, using data from Austrian RA patients. We externally validated the results on an independent dataset from the Erlangen Hospital. To improve the reliability of probability estimates for actionable risk stratification, we employed calibration techniques, including Platt scaling, Isotonic regression, Beta calibration, and Spline calibration. We generated calibration curves to assess and visualize the alignment between predicted probabilities and observed outcomes. In addition, we used SHapley Additive exPlanations (SHAP) to analyze the contributions of different patient characteristics to the prediction of RA remission. AdaBoost demonstrated stronger performance than the other models, achieving an accuracy of 85.71% and a Brier score of 0.13 with isotonic regression calibration. SHAP identified DAS28, visual analog scales (VAS), age, and swollen joint count (SJC) as important characteristics for the prediction of RA remission. We also stratified patients into low-, medium-, and high-risk categories based on model predictions to support follow-up scheduling and treatment prioritization. Our framework predicts RA remission before the initiation of bDMARD therapy. It enables personalized care, actionable risk stratification, and optimized resource allocation. Its robustness was validated on two different individual cohort datasets, which highlights its potential for integration into routine clinical workflows.

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来源期刊
Scientific Reports
Scientific Reports Natural Science Disciplines-
CiteScore
7.50
自引率
4.30%
发文量
19567
审稿时长
3.9 months
期刊介绍: We publish original research from all areas of the natural sciences, psychology, medicine and engineering. You can learn more about what we publish by browsing our specific scientific subject areas below or explore Scientific Reports by browsing all articles and collections. Scientific Reports has a 2-year impact factor: 4.380 (2021), and is the 6th most-cited journal in the world, with more than 540,000 citations in 2020 (Clarivate Analytics, 2021). •Engineering Engineering covers all aspects of engineering, technology, and applied science. It plays a crucial role in the development of technologies to address some of the world''s biggest challenges, helping to save lives and improve the way we live. •Physical sciences Physical sciences are those academic disciplines that aim to uncover the underlying laws of nature — often written in the language of mathematics. It is a collective term for areas of study including astronomy, chemistry, materials science and physics. •Earth and environmental sciences Earth and environmental sciences cover all aspects of Earth and planetary science and broadly encompass solid Earth processes, surface and atmospheric dynamics, Earth system history, climate and climate change, marine and freshwater systems, and ecology. It also considers the interactions between humans and these systems. •Biological sciences Biological sciences encompass all the divisions of natural sciences examining various aspects of vital processes. The concept includes anatomy, physiology, cell biology, biochemistry and biophysics, and covers all organisms from microorganisms, animals to plants. •Health sciences The health sciences study health, disease and healthcare. This field of study aims to develop knowledge, interventions and technology for use in healthcare to improve the treatment of patients.
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