四种天冬酰胺酶的理化品质评价。

IF 2.6 3区 综合性期刊 Q1 MULTIDISCIPLINARY SCIENCES
PLoS ONE Pub Date : 2025-06-16 eCollection Date: 2025-01-01 DOI:10.1371/journal.pone.0326106
Vanessa Radtke, Thorsten König, Christoph Radcke, Ulf Bergmann, Rene Eichler, Katja J Pohl, Arndt Schnuchel
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引用次数: 0

摘要

l -天冬酰胺酶(ASNases)用于治疗急性淋巴细胞白血病。一些治疗性天冬酰胺酶产品有质量问题的报道,特别是在中等收入国家生产的产品。这些产物可能表现出效力降低和/或特异性活性降低,或杂质水平升高,如宿主细胞蛋白。在本研究中,详细比较了四种未用聚乙二醇修饰的ASNase制剂的质量:Spectrila®,Celginase™,Bionase®和L-Aspase®。分析样品的蛋白质含量、杂质和酶活性。各种色谱方法以及质谱法被用来评估纯度和鉴定。样品蛋白含量、宿主细胞蛋白和酶活性显示一些结果超出Celginase™和Bionase®的目标范围。这些ASNase制剂也显示出可检测的内毒素水平。在凝胶电泳中,发现了Bionase®的附加条带。尺寸排除层析显示Bionase®和L-Aspase®的高分子量和低分子量物种增加,反相层析显示Bionase®的亲水性和疏水性物种增加。在毛细管区带电泳中,发现L-Aspase®的保留时间增加,Bionase®、Celginase™和L-Aspase®的电荷变异水平增加。ASNase的质量标准对于确保患者安全和产品疗效至关重要,因为效力和特异性活性的降低可能影响急性淋巴细胞白血病治疗的疗效,而杂质的增加可能影响免疫原性。在本研究中测试的四种ASNase制剂中,只有Spectrila®没有引起任何质量问题。其他三种产品存在质量问题,不符合欧美注射剂药品开发指南中规定的既定质量要求。
本文章由计算机程序翻译,如有差异,请以英文原文为准。

Physicochemical quality assessment of four asparaginases.

Physicochemical quality assessment of four asparaginases.

Physicochemical quality assessment of four asparaginases.

Physicochemical quality assessment of four asparaginases.

L-Asparaginases (ASNases) are used for the treatment of acute lymphoblastic leukaemia. There are reports of quality problems for some therapeutic asparaginase products, especially those manufactured in middle-income countries. These products may exhibit decreased potency and/or decreased specific activity, or an elevated level of impurities such as host cell proteins. In this study, four different ASNase preparations that were not modified with polyethylene glycol were compared in detail regarding their quality: Spectrila®, Celginase™, Bionase®, and L-Aspase®. Samples were analyzed for protein content, impurities, and enzyme activity. Various chromatographic methods as well as mass spectrometry were used to assess purity and identity. Sample protein content, host cell protein, and enzyme activity showed some results that were out of target range for Celginase™ and Bionase®. These ASNase preparations also showed detectable levels of endotoxins. In gel electrophoresis, additional bands were found for Bionase®. Size exclusion chromatography showed increased high and low molecular weight species for Bionase® and L-Aspase®, and reversed-phase chromatography showed increased hydrophilic and hydrophobic species for Bionase®. In capillary zone electrophoresis, increased retention time for L-Aspase® and increased levels of charge variants for Bionase®, Celginase™, and L-Aspase® were seen. ASNase quality standards are crucial to ensure patient safety and product efficacy, as decreased potency and specific activity may affect efficacy in acute lymphoblastic leukaemia treatment, and increased impurities may affect immunogenicity. Out of four ASNase preparations tested in this study, only Spectrila® did not raise any quality concerns. The other three products exhibited quality problems, rendering them unsuitable according to established quality requirements defined in European and US guidelines for pharmaceutical development of parenteral drug products.

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来源期刊
PLoS ONE
PLoS ONE 生物-生物学
CiteScore
6.20
自引率
5.40%
发文量
14242
审稿时长
3.7 months
期刊介绍: PLOS ONE is an international, peer-reviewed, open-access, online publication. PLOS ONE welcomes reports on primary research from any scientific discipline. It provides: * Open-access—freely accessible online, authors retain copyright * Fast publication times * Peer review by expert, practicing researchers * Post-publication tools to indicate quality and impact * Community-based dialogue on articles * Worldwide media coverage
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