Victoria Fanucci, Dhaval Chauhan, Nita Ray Chaudhuri, Hemal M Nayak, Utkarsh Kohli
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引用次数: 0
摘要
桥粒蛋白是桥粒的核心成分,由DSP (Online Mendelian Inheritance in Man [OMIM]: 125647)编码。DSP的突变与心律失常性心肌病(ACM)和其他皮肤疾病的发展有关。我们报告了一例罕见的左显性心律失常性心肌病(LDACM),患者为一名16岁的女孩,患有一种新的家族移帧DSP c.4751_4752del (p.a ala1584valfs *42, rs2113694794)突变。患者出现持续性室性心动过速,经胺碘酮控制,需要植入双室经静脉除颤器预防心源性猝死(SCD),因其5年不良后果风险估计为25%。考虑到ACM的后遗症包括心衰(HF)、室性心律失常(VA)和SCD的早期发展,该患者的研究结果强调了将ACM纳入心肌炎患者鉴别诊断的重要性。
A novel familial pathogenic desmoplakin (DSP) gene mutation (c.4751_4752del) presenting as "hot-phase" left-dominant arrhythmogenic cardiomyopathy.
Desmoplakin, encoded by DSP (Online Mendelian Inheritance in Man [OMIM]: 125647), is a central component of desmosomes. Mutations in DSP have been implicated in the development of arrhythmogenic cardiomyopathy (ACM) and other cutaneous conditions. We report on a rare, myocarditis-like presentation of left-dominant arrhythmogenic cardiomyopathy (LDACM) in a 16-year-old girl with a novel familial frame-shift DSP c.4751_4752del (p.Ala1584Valfs *42, rs2113694794) mutation. The patient developed sustained ventricular tachycardia, which was controlled with amiodarone and required implantation of a dual-chamber transvenous defibrillator for sudden cardiac death (SCD) prophylaxis as her 5-year risk of adverse outcomes was estimated to be 25%. The findings in this patient highlight the importance of including ACM in the differential diagnosis for patients presenting with myocarditis, given that the sequelae of ACM include early development of heart failure (HF), ventricular arrhythmia (VA), and SCD.
期刊介绍:
Research advances have contributed to improved outcomes across all specialties, but the rate of advancement in cardiology has been exceptional. Concurrently, the population of patients with cardiac conditions continues to grow and greater public awareness has increased patients" expectations of new drugs and devices. Future Cardiology (ISSN 1479-6678) reflects this new era of cardiology and highlights the new molecular approach to advancing cardiovascular therapy. Coverage will also reflect the major technological advances in bioengineering in cardiology in terms of advanced and robust devices, miniaturization, imaging, system modeling and information management issues.