评估 9 号腺病毒血清型 (AAV9) 的血清流行率，为 RIDGE™-1 做准备，RIDGE™-1 是一项 1b 期首次人体试验，目的是评估 TN-401 基因疗法在 PKP2 相关性致心律失常性右室心肌病 (ARVC) 成人患者中的安全性和有效性。

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