{"title":"化学遗传工具及其在神经精神疾病研究中的应用。","authors":"M Neřoldová, A Stuchlík","doi":"10.33549/physiolres.935401","DOIUrl":null,"url":null,"abstract":"<p><p>Chemogenetics is a newly developed set of tools that allow for selective manipulation of cell activity. They consist of a receptor mutated irresponsive to endogenous ligands and a synthetic ligand that does not interact with the wild-type receptors. Many different types of these receptors and their respective ligands for inhibiting or excitating neuronal subpopulations were designed in the past few decades. It has been mainly the G-protein coupled receptors (GPCRs) selectively responding to clozapine-N-oxide (CNO), namely Designer Receptors Exclusively Activated by Designer Drugs (DREADDs), that have been employed in research. Chemogenetics offers great possibilities since the activity of the receptors is reversible, inducible on demand by the ligand, and non-invasive. Also, specific groups or types of neurons can be selectively manipulated thanks to the delivery by viral vectors. The effect of the chemogenetic receptors on neurons lasts longer, and even chronic activation can be achieved. That can be useful for behavioral testing. The great advantage of chemogenetic tools is especially apparent in research on brain diseases since they can manipulate whole neuronal circuits and connections between different brain areas. Many psychiatric or other brain diseases revolve around the dysfunction of specific brain networks. Therefore, chemogenetics presents a powerful tool for investigating the underlying mechanisms causing the disease and revealing the link between the circuit dysfunction and the behavioral or cognitive symptoms observed in patients. 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引用次数: 0
摘要
化学遗传学是一套新开发的工具,可以选择性地操纵细胞活性。它们由对内源性配体无反应的突变受体和不与野生型受体相互作用的合成配体组成。在过去几十年中,人们设计出了许多不同类型的受体及其各自的配体,用于抑制或兴奋神经元亚群。研究中采用的主要是对氯氮平-氧化物(CNO)有选择性反应的 G 蛋白偶联受体(GPCRs),即专门由 Designer Drugs 激活的 Designer Receptors Exclusively Activated by Designer Drugs(DREADDs)。化学遗传学提供了巨大的可能性,因为受体的活性是可逆的,可根据配体的要求进行诱导,而且是非侵入性的。此外,通过病毒载体的传递,还可以选择性地操纵特定群体或类型的神经元。化学基因受体对神经元的作用持续时间更长,甚至可以实现慢性激活。这对行为测试非常有用。化学遗传工具的巨大优势在脑部疾病研究中尤为明显,因为它们可以操纵整个神经元回路和不同脑区之间的连接。许多精神疾病或其他脑部疾病都与特定脑部网络的功能障碍有关。因此,化学遗传学是一种强大的工具,可用于研究导致疾病的潜在机制,并揭示回路功能障碍与患者行为或认知症状之间的联系。它还有助于开发更有效的治疗方法。
Chemogenetic Tools and their Use in Studies of Neuropsychiatric Disorders.
Chemogenetics is a newly developed set of tools that allow for selective manipulation of cell activity. They consist of a receptor mutated irresponsive to endogenous ligands and a synthetic ligand that does not interact with the wild-type receptors. Many different types of these receptors and their respective ligands for inhibiting or excitating neuronal subpopulations were designed in the past few decades. It has been mainly the G-protein coupled receptors (GPCRs) selectively responding to clozapine-N-oxide (CNO), namely Designer Receptors Exclusively Activated by Designer Drugs (DREADDs), that have been employed in research. Chemogenetics offers great possibilities since the activity of the receptors is reversible, inducible on demand by the ligand, and non-invasive. Also, specific groups or types of neurons can be selectively manipulated thanks to the delivery by viral vectors. The effect of the chemogenetic receptors on neurons lasts longer, and even chronic activation can be achieved. That can be useful for behavioral testing. The great advantage of chemogenetic tools is especially apparent in research on brain diseases since they can manipulate whole neuronal circuits and connections between different brain areas. Many psychiatric or other brain diseases revolve around the dysfunction of specific brain networks. Therefore, chemogenetics presents a powerful tool for investigating the underlying mechanisms causing the disease and revealing the link between the circuit dysfunction and the behavioral or cognitive symptoms observed in patients. It could also contribute to the development of more effective treatments.
期刊介绍:
Accounts of Chemical Research presents short, concise and critical articles offering easy-to-read overviews of basic research and applications in all areas of chemistry and biochemistry. These short reviews focus on research from the author’s own laboratory and are designed to teach the reader about a research project. In addition, Accounts of Chemical Research publishes commentaries that give an informed opinion on a current research problem. Special Issues online are devoted to a single topic of unusual activity and significance.
Accounts of Chemical Research replaces the traditional article abstract with an article "Conspectus." These entries synopsize the research affording the reader a closer look at the content and significance of an article. Through this provision of a more detailed description of the article contents, the Conspectus enhances the article's discoverability by search engines and the exposure for the research.