与 PACS2 致病变异有关的婴儿期移动性局灶性癫痫发作

Sukanya Vrushabhendra , Alan Taylor , Kate Flynn , Pawan Kashyape
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引用次数: 0

摘要

婴儿癫痫伴移灶性发作(EIMFS)是一种遗传异质性疾病,表现为早期婴儿癫痫性脑病。在此,我们报告了一个典型的与发育和癫痫性脑病相关的 PACS2 致病变异体,该变异体的婴儿临床和电图检查结果提示为 EIMFS,但该婴儿对小剂量卡马西平反应良好,并达到了正常的发育里程碑。该病例突显了复发性 PACS2 变异的一种意想不到的表型表现,并为这种临床表现提出了一种有效的治疗方法。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Migrating focal seizures of infancy associated with pathogenic variants in PACS2

Epilepsy of infancy with migrating focal seizures (EIMFS) is a genetically heterogeneous disorder presenting with early infantile epileptic encephalopathy. Here we report a PACS2 pathogenic variant typically associated with a developmental and epileptic encephalopathy in an infant presenting with clinical and electrographic findings suggestive of EIMFS who, however, responded well to low dose Carbamazepine and achieved normal developmental milestones. This case highlights an unexpected phenotypic presentation of a recurrent PACS2 variant and suggests an effective therapeutic approach to this clinical presentation.

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