蛋白质病的治疗方法。

3区 生物学 Q2 Biochemistry, Genetics and Molecular Biology
Mohsen Nabi Afjadi, Bahareh Dabirmanesh, Vladimir N Uversky
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引用次数: 0

摘要

淀粉样变性病、蛋白病或淀粉样变性病等一系列疾病的特征是在许多器官和组织中积累含有交叉β片淀粉样纤维的异常蛋白质聚集体。这些纤维通常是由不正常形成或折叠的蛋白质构成的。目前,淀粉样蛋白疾病的大多数治疗方法都侧重于控制症状,而不是治愈或预防潜在的疾病过程。然而,随着我们对淀粉样蛋白疾病生物学认识的不断深入,针对淀粉样蛋白纤维的出现和积累的创新疗法应运而生。这些疗法包括使用小分子化合物、单克隆抗体、基因疗法等。最后,即使淀粉样蛋白疾病的大多数疗法都是对症治疗,但对这些疾病背后的生物学的更深入研究正在为潜在疗法确定新的靶点,并为未来开发更有效的疗法铺平道路。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Therapeutic approaches in proteinopathies.

A family of maladies known as amyloid disorders, proteinopathy, or amyloidosis, are characterized by the accumulation of abnormal protein aggregates containing cross-β-sheet amyloid fibrils in many organs and tissues. Often, proteins that have been improperly formed or folded make up these fibrils. Nowadays, most treatments for amyloid illness focus on managing symptoms rather than curing or preventing the underlying disease process. However, recent advances in our understanding of the biology of amyloid diseases have led to the development of innovative therapies that target the emergence and accumulation of amyloid fibrils. Examples of these treatments include the use of small compounds, monoclonal antibodies, gene therapy, and others. In the end, even if the majority of therapies for amyloid diseases are symptomatic, greater research into the biology behind these disorders is identifying new targets for potential therapy and paving the way for the development of more effective treatments in the future.

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来源期刊
CiteScore
6.90
自引率
0.00%
发文量
0
审稿时长
>12 weeks
期刊介绍: Progress in Molecular Biology and Translational Science (PMBTS) provides in-depth reviews on topics of exceptional scientific importance. If today you read an Article or Letter in Nature or a Research Article or Report in Science reporting findings of exceptional importance, you likely will find comprehensive coverage of that research area in a future PMBTS volume.
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