视网膜疾病

IF 7.8 2区医学 Q1 MEDICINE, RESEARCH & EXPERIMENTAL

Cold Spring Harbor perspectives in medicine Pub Date : 2024-04-02 DOI:10.1101/cshperspect.a041728

José-Alain Sahel, Eyal Banin, Jean Bennett, Jacque L. Duncan, Botond Roska

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引用次数: 0

摘要

由遗传或环境因素引起的视网膜疾病会造成严重的视力损伤，并常常导致失明。过去十年间，我们对这些疾病的生物学基础的认识取得了飞速进步，基因和细胞疗法也取得了重大进展。监管方面的挑战依然存在，但我们有理由希望，创造性的方法将在不久的将来为这些疾病带来安全有效的突破性疗法。

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Retinal Disorders

Retinal disorders caused by genetic or environmental factors cause severe visual impairment and often result in blindness. The past ten years have seen rapid progress in our understanding of the biological basis of these conditions, as well as significant advances towards gene and cell-based therapies. Regulatory challenges remain, but there is reason to hope that creative approaches will lead to safe and effective breakthrough treatments for these conditions in the near future.

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来源期刊

Cold Spring Harbor perspectives in medicine MEDICINE, RESEARCH & EXPERIMENTAL-

CiteScore

14.30

自引率

1.90%

发文量

审稿时长

4-8 weeks

期刊介绍： Cold Spring Harbor Perspectives in Medicine is a monthly online publication comprising reviews on different aspects of a variety of diseases, covering everything from the molecular and cellular bases of disease to translational medicine and new therapeutic strategies. Cold Spring Harbor Perspectives in Medicine is thus unmatched in its depth of coverage and represents an essential source where readers can find informed surveys and critical discussion of advances in molecular medicine.