DNAI1 mRNA结构优化治疗原发性纤毛运动障碍

M. Hennig, D. Ishimaru, D. Liston, R. Bhattacharjee, M. Sidhu, J. Poniatowski, J.E. Casillas, H. Lister, S. Comini, V. Kharitonov, D. J. Lockhart, B. Wustman
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Optimization of DNAI1 mRNA Constructs to Treat Primary Ciliary Dyskinesia
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