[19]在hd临床前模型中,多唾液酸代谢缺陷可能是一个有效的治疗靶点

G. Pepe, L. Capocci, F. Marracino, S. Moons, Aynur Sönmez, Karolina Świtońska-Kurkowska, P. Scarselli, Clotilde Di Cicco, M. Figiel, T. Boltje, R. Parlato, A. D. Pardo, V. Maglione
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I19 The defective metabolism of polysialic acid (polysia) may represent an effective therapeutic target in hd pre-clinical models
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