I06 Allele-selective inhibition of mutant htt transcription throughout the brain after subcutaneous administration of a patrol™-enabled investigational genetic therapy in the r6/2 Huntington’s disease transgenic mouse model
R. Friedlander, V. Caro, D. Carlisle, N. Monks, Dani M. Stoltzfus, Natasha L Bennett, Y. Suofu, Jinho Kim, Fang Li, Xiaomin Wang, Stacy Yeh, O. V. Baranov, S. Baranov, Barry A. Badeau, Jeremy Gleaton, Gabriel A Cintrón-Rosado, Ryan R Dyer, D. Stephan, W. R. Mann, Sandra Rojas-Caro
{"title":"I06 Allele-selective inhibition of mutant htt transcription throughout the brain after subcutaneous administration of a patrol™-enabled investigational genetic therapy in the r6/2 Huntington’s disease transgenic mouse model","authors":"R. Friedlander, V. Caro, D. Carlisle, N. Monks, Dani M. Stoltzfus, Natasha L Bennett, Y. Suofu, Jinho Kim, Fang Li, Xiaomin Wang, Stacy Yeh, O. V. Baranov, S. Baranov, Barry A. Badeau, Jeremy Gleaton, Gabriel A Cintrón-Rosado, Ryan R Dyer, D. Stephan, W. R. Mann, Sandra Rojas-Caro","doi":"10.1136/jnnp-2022-ehdn.232","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":444837,"journal":{"name":"I: Experimental therapeutics – preclinical","volume":"1 1","pages":"0"},"PeriodicalIF":0.0000,"publicationDate":"2022-09-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"I: Experimental therapeutics – preclinical","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1136/jnnp-2022-ehdn.232","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}