A. Rashnonejad, Gholamhossein Amini Chermahini, Cumhur Gündüz, H. Onay, A. Aykut, B. Durmaz, M. Baka, Q. Su, G. Gao, F. Özkınay
{"title":"单次注射重组AAV9挽救小鼠SMA表型的胎儿基因治疗。","authors":"A. Rashnonejad, Gholamhossein Amini Chermahini, Cumhur Gündüz, H. Onay, A. Aykut, B. Durmaz, M. Baka, Q. Su, G. Gao, F. Özkınay","doi":"10.1016/j.ymthe.2019.08.017","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":19039,"journal":{"name":"Molecular Therapy: the Journal of the American Society of Gene Therapy","volume":"51 1","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2019-12-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"23","resultStr":"{\"title\":\"Fetal Gene Therapy Using a Single Injection of Recombinant AAV9 Rescued SMA Phenotype in Mice.\",\"authors\":\"A. Rashnonejad, Gholamhossein Amini Chermahini, Cumhur Gündüz, H. Onay, A. Aykut, B. Durmaz, M. Baka, Q. Su, G. Gao, F. Özkınay\",\"doi\":\"10.1016/j.ymthe.2019.08.017\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"\",\"PeriodicalId\":19039,\"journal\":{\"name\":\"Molecular Therapy: the Journal of the American Society of Gene Therapy\",\"volume\":\"51 1\",\"pages\":\"\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2019-12-01\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"23\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"Molecular Therapy: the Journal of the American Society of Gene Therapy\",\"FirstCategoryId\":\"1085\",\"ListUrlMain\":\"https://doi.org/10.1016/j.ymthe.2019.08.017\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"\",\"JCRName\":\"\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Therapy: the Journal of the American Society of Gene Therapy","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymthe.2019.08.017","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}