在经典半乳糖血症小鼠模型中,基于mrna的新疗法可减少有毒半乳糖代谢物并克服半乳糖敏感性。

B. Balakrishnan, D. An, Vi Nguyen, Christine DeAntonis, P. Martini, K. Lai
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引用次数: 34

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本文章由计算机程序翻译,如有差异,请以英文原文为准。
Novel mRNA-Based Therapy Reduces Toxic Galactose Metabolites and Overcomes Galactose Sensitivity in a Mouse Model of Classic Galactosemia.
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