墨西哥先天性中间代谢错误患者队列中33年来的差异和未满足的新生儿筛查需求综述。

IF 4 Q1 GENETICS & HEREDITY
Isabel Ibarra-González, Cynthia Fernández-Lainez, Marcela Vela-Amieva, Sara Guillén-López, Leticia Belmont-Martínez, Lizbeth López-Mejía, Rosa Itzel Carrillo-Nieto, Nidia Alejandra Guillén-Zaragoza
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引用次数: 0

摘要

通过扩大新生儿筛查(NBS)进行早期诊断的进展主要在发达国家取得,而中低收入国家的人口获得早期诊断的机会很少,这导致了差异。在墨西哥扩大NBS不是强制性的。在此,我们概述了一组墨西哥先天性中间代谢错误(IEiM)患者的差异和未满足的NBS需求,强调了获得诊断的历程。我们对一个国家参考中心的IEiM患者历史队列进行了一项回顾性观察性研究。共纳入924名IEiM患者。尽管72.5%的疾病可以通过扩大NBS检测到,但只有35.4%的患者接受了筛查。未筛查组的死亡率几乎是筛查组的两倍。患者的中位诊断延迟为4个月,考虑到为了防止残疾和死亡,这些疾病必须在生命的最初几天得到治疗,这是不可接受的长时间。患者不得不长途跋涉前往我们的参考中心,这导致了他们无法接受的诊断之旅。这项研究强调,迫切需要在墨西哥制定一个更新、扩大的国家统计局计划,并采取充分的后续行动,推动建立地区医疗保健中心。我们还提供了令人信服的证据,这些证据可能对监督中等收入和低收入国家受IEiM影响的个人的公共卫生举措的决策者有价值。
本文章由计算机程序翻译,如有差异,请以英文原文为准。

A Review of Disparities and Unmet Newborn Screening Needs over 33 Years in a Cohort of Mexican Patients with Inborn Errors of Intermediary Metabolism.

A Review of Disparities and Unmet Newborn Screening Needs over 33 Years in a Cohort of Mexican Patients with Inborn Errors of Intermediary Metabolism.

A Review of Disparities and Unmet Newborn Screening Needs over 33 Years in a Cohort of Mexican Patients with Inborn Errors of Intermediary Metabolism.

A Review of Disparities and Unmet Newborn Screening Needs over 33 Years in a Cohort of Mexican Patients with Inborn Errors of Intermediary Metabolism.

Advances in an early diagnosis by expanded newborn screening (NBS) have been achieved mainly in developed countries, while populations of middle- and low-income countries have poor access, leading to disparities. Expanded NBS in Mexico is not mandatory. Herein, we present an overview of the differences and unmet NBS needs of a group of Mexican patients with inborn errors of intermediary metabolism (IEiM), emphasizing the odyssey experienced to reach a diagnosis. We conducted a retrospective observational study of a historical cohort of patients with IEiM from a national reference center. A total of 924 patients with IEiM were included. Although 72.5% of the diseases identified are detectable by expanded NBS, only 35.4% of the patients were screened. The mortality in the unscreened group was almost two-fold higher than that in the screened group. Patients experienced a median diagnostic delay of 4 months, which is unacceptably long considering that to prevent disability and death, these disorders must be treated in the first days of life. Patients had to travel long distances to our reference center, contributing to their unacceptable diagnostic odyssey. This study highlights the urgent need to have an updated, expanded NBS program with adequate follow up in Mexico and promote the creation of regional medical care centers. We also provide compelling evidence that could prove valuable to decision makers overseeing public health initiatives for individuals impacted by IEiM from middle- and low-income countries.

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来源期刊
International Journal of Neonatal Screening
International Journal of Neonatal Screening Medicine-Pediatrics, Perinatology and Child Health
CiteScore
6.70
自引率
20.00%
发文量
56
审稿时长
11 weeks
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