基因治疗的临床应用:新出现的机会和当前的限制

Mccabe E.R.B.
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引用次数: 10

摘要

人类基因治疗方案已经获得批准,一些调查试验正在进行中。虽然体细胞基因治疗比种系治疗更受青睐,但必须认识到体细胞的转化可能在不经意间发生。体外和体内方法为遗传干预提供了两种不同的策略,并在治疗先天性代谢错误、脑肿瘤和其他神经系统疾病、艾滋病和其他传染病的背景下进行了讨论。目前的技术看起来很有希望,但在常规应用基因治疗之前仍然存在严重的局限性。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Clinical Application of Gene Therapy: Emerging Opportunities and Current Limitations
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