{"title":"IDPs的过渡态构象:在人胰淀素(hIAPP)中的应用。","authors":"Nicholas A Carton, Nicolae-Viorel Buchete","doi":"10.1021/acs.jpcb.5c05357","DOIUrl":null,"url":null,"abstract":"<p><p>Human islet amyloid polypeptide (hIAPP, a.k.a. amylin) aggregation is involved in the pathogenesis of type 2 diabetes, yet no effective inhibitors of fibril formation are currently available. In this study, we examine the conformational transitions of hIAPP monomers across distinct molecular environments (i.e., lipids, water, and amyloid fibrils), to probe key features, such as transition states across the complex free energy landscape of the amyloidization pathway. Using unbiased molecular dynamics simulations of monomeric amylin, we apply relative RMSD values as putative reaction coordinates to identify and assess transition state ensemble (TSE) membership of monomeric amylin conformations. TSE conformations are high-value drug targets located at the probabilistic midpoint between aggregation-prone and helical-rich reference states. Using relative RMSD, we validate a transition state candidate as a TSE member and identify additional kinetically similar amylin conformations. Segment-level analysis offers insight into early stage branching along the aggregation pathway. These findings establish relative RMSD as a useful parameter for characterizing transitions in amylin and other intrinsically disordered proteins.</p>","PeriodicalId":60,"journal":{"name":"The Journal of Physical Chemistry B","volume":" ","pages":""},"PeriodicalIF":2.9000,"publicationDate":"2025-10-13","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"Transition State Conformations for IDPs: Application to Human Amylin (hIAPP).\",\"authors\":\"Nicholas A Carton, Nicolae-Viorel Buchete\",\"doi\":\"10.1021/acs.jpcb.5c05357\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"<p><p>Human islet amyloid polypeptide (hIAPP, a.k.a. amylin) aggregation is involved in the pathogenesis of type 2 diabetes, yet no effective inhibitors of fibril formation are currently available. In this study, we examine the conformational transitions of hIAPP monomers across distinct molecular environments (i.e., lipids, water, and amyloid fibrils), to probe key features, such as transition states across the complex free energy landscape of the amyloidization pathway. Using unbiased molecular dynamics simulations of monomeric amylin, we apply relative RMSD values as putative reaction coordinates to identify and assess transition state ensemble (TSE) membership of monomeric amylin conformations. TSE conformations are high-value drug targets located at the probabilistic midpoint between aggregation-prone and helical-rich reference states. Using relative RMSD, we validate a transition state candidate as a TSE member and identify additional kinetically similar amylin conformations. Segment-level analysis offers insight into early stage branching along the aggregation pathway. These findings establish relative RMSD as a useful parameter for characterizing transitions in amylin and other intrinsically disordered proteins.</p>\",\"PeriodicalId\":60,\"journal\":{\"name\":\"The Journal of Physical Chemistry B\",\"volume\":\" \",\"pages\":\"\"},\"PeriodicalIF\":2.9000,\"publicationDate\":\"2025-10-13\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"The Journal of Physical Chemistry B\",\"FirstCategoryId\":\"1\",\"ListUrlMain\":\"https://doi.org/10.1021/acs.jpcb.5c05357\",\"RegionNum\":2,\"RegionCategory\":\"化学\",\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"Q3\",\"JCRName\":\"CHEMISTRY, PHYSICAL\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"The Journal of Physical Chemistry B","FirstCategoryId":"1","ListUrlMain":"https://doi.org/10.1021/acs.jpcb.5c05357","RegionNum":2,"RegionCategory":"化学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"Q3","JCRName":"CHEMISTRY, PHYSICAL","Score":null,"Total":0}
Transition State Conformations for IDPs: Application to Human Amylin (hIAPP).
Human islet amyloid polypeptide (hIAPP, a.k.a. amylin) aggregation is involved in the pathogenesis of type 2 diabetes, yet no effective inhibitors of fibril formation are currently available. In this study, we examine the conformational transitions of hIAPP monomers across distinct molecular environments (i.e., lipids, water, and amyloid fibrils), to probe key features, such as transition states across the complex free energy landscape of the amyloidization pathway. Using unbiased molecular dynamics simulations of monomeric amylin, we apply relative RMSD values as putative reaction coordinates to identify and assess transition state ensemble (TSE) membership of monomeric amylin conformations. TSE conformations are high-value drug targets located at the probabilistic midpoint between aggregation-prone and helical-rich reference states. Using relative RMSD, we validate a transition state candidate as a TSE member and identify additional kinetically similar amylin conformations. Segment-level analysis offers insight into early stage branching along the aggregation pathway. These findings establish relative RMSD as a useful parameter for characterizing transitions in amylin and other intrinsically disordered proteins.
期刊介绍:
An essential criterion for acceptance of research articles in the journal is that they provide new physical insight. Please refer to the New Physical Insights virtual issue on what constitutes new physical insight. Manuscripts that are essentially reporting data or applications of data are, in general, not suitable for publication in JPC B.