Rebecca K Voss,Victor B Pastor Loyola,Maria F Cardenas,Priya Kumar,Jamie L Maciaszek,Maria Namwanje,Jing Ma,Jennifer L Neary,Meiling Jin,Masayuki Umeda,Mark R Wilkinson,Debbie Payne-Turner,Mohammad K Eldomery,Jingqun Ma,Jiali Gu,Jim Dalton,Samantha Melton,Yen-Chun Liu,Scott Foy,Michael Rusch,David A Wheeler,Jinghui Zhang,Kim E Nichols,Seth E Karol,Hiroto Inaba,Raul Ribeiro,Jeffrey E Rubnitz,Jeffery M Klco,Lu Wang
{"title":"综合全基因组和转录组测序作为儿童和青少年急性髓性白血病诊断和风险评估框架的临床经验。","authors":"Rebecca K Voss,Victor B Pastor Loyola,Maria F Cardenas,Priya Kumar,Jamie L Maciaszek,Maria Namwanje,Jing Ma,Jennifer L Neary,Meiling Jin,Masayuki Umeda,Mark R Wilkinson,Debbie Payne-Turner,Mohammad K Eldomery,Jingqun Ma,Jiali Gu,Jim Dalton,Samantha Melton,Yen-Chun Liu,Scott Foy,Michael Rusch,David A Wheeler,Jinghui Zhang,Kim E Nichols,Seth E Karol,Hiroto Inaba,Raul Ribeiro,Jeffrey E Rubnitz,Jeffery M Klco,Lu Wang","doi":"10.1038/s41375-025-02774-5","DOIUrl":null,"url":null,"abstract":"Pediatric acute myeloid leukemia (AML) exhibits distinct genetic characteristics, including unique driver alterations and mutations with prognostic and therapeutic implications. Cytogenetics study, along with Next Generation Sequencing (NGS) panel testing, have long been the standard for molecular diagnosis of AML. While these approaches enable diagnosis and prognosis determination in most cases, they have limitations-particularly in detecting emerging rare, recurrent genetic abnormalities. In this study, we systematically reviewed our real-time clinical experience with the diagnostic workup of pediatric AML using an integrated whole genome and whole transcriptome sequencing (iWGS-WTS) approach and compared the test results obtained from various methodologies, including whole genome sequencing (WGS), whole exome sequencing (WES), whole transcriptome sequencing (WTS), iWGS-WTS, cytogenetics, and targeted panel NGS. Our findings demonstrate that the iWGS-WTS approach improves the identification of clinically relevant genetic alterations, enhancing precise disease classification and risk assessment. Additionally, the iWGS-WTS approach streamlines sample acquisition and reduces testing redundancy, positioning it as a practical and superior alternative to traditional diagnostic methods in pediatric AML management.","PeriodicalId":18109,"journal":{"name":"Leukemia","volume":"107 1","pages":""},"PeriodicalIF":13.4000,"publicationDate":"2025-10-07","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"Clinical experience of using integrated whole genome and transcriptome sequencing as a framework for pediatric and adolescent acute myeloid leukemia diagnosis and risk assessment.\",\"authors\":\"Rebecca K Voss,Victor B Pastor Loyola,Maria F Cardenas,Priya Kumar,Jamie L Maciaszek,Maria Namwanje,Jing Ma,Jennifer L Neary,Meiling Jin,Masayuki Umeda,Mark R Wilkinson,Debbie Payne-Turner,Mohammad K Eldomery,Jingqun Ma,Jiali Gu,Jim Dalton,Samantha Melton,Yen-Chun Liu,Scott Foy,Michael Rusch,David A Wheeler,Jinghui Zhang,Kim E Nichols,Seth E Karol,Hiroto Inaba,Raul Ribeiro,Jeffrey E Rubnitz,Jeffery M Klco,Lu Wang\",\"doi\":\"10.1038/s41375-025-02774-5\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"Pediatric acute myeloid leukemia (AML) exhibits distinct genetic characteristics, including unique driver alterations and mutations with prognostic and therapeutic implications. 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Clinical experience of using integrated whole genome and transcriptome sequencing as a framework for pediatric and adolescent acute myeloid leukemia diagnosis and risk assessment.
Pediatric acute myeloid leukemia (AML) exhibits distinct genetic characteristics, including unique driver alterations and mutations with prognostic and therapeutic implications. Cytogenetics study, along with Next Generation Sequencing (NGS) panel testing, have long been the standard for molecular diagnosis of AML. While these approaches enable diagnosis and prognosis determination in most cases, they have limitations-particularly in detecting emerging rare, recurrent genetic abnormalities. In this study, we systematically reviewed our real-time clinical experience with the diagnostic workup of pediatric AML using an integrated whole genome and whole transcriptome sequencing (iWGS-WTS) approach and compared the test results obtained from various methodologies, including whole genome sequencing (WGS), whole exome sequencing (WES), whole transcriptome sequencing (WTS), iWGS-WTS, cytogenetics, and targeted panel NGS. Our findings demonstrate that the iWGS-WTS approach improves the identification of clinically relevant genetic alterations, enhancing precise disease classification and risk assessment. Additionally, the iWGS-WTS approach streamlines sample acquisition and reduces testing redundancy, positioning it as a practical and superior alternative to traditional diagnostic methods in pediatric AML management.
期刊介绍:
Title: Leukemia
Journal Overview:
Publishes high-quality, peer-reviewed research
Covers all aspects of research and treatment of leukemia and allied diseases
Includes studies of normal hemopoiesis due to comparative relevance
Topics of Interest:
Oncogenes
Growth factors
Stem cells
Leukemia genomics
Cell cycle
Signal transduction
Molecular targets for therapy
And more
Content Types:
Original research articles
Reviews
Letters
Correspondence
Comments elaborating on significant advances and covering topical issues