基于Beta分布设计免疫研究的实用框架。

IF 1.8 4区 医学 Q3 MATHEMATICAL & COMPUTATIONAL BIOLOGY
Stefan Embacher, Andrea Berghold, Kirsten Maertens, Sereina A Herzog
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引用次数: 0

摘要

一个优化设计的实验可以更快地获得结果,成本更低,观察次数更少,因此对于最大限度地提高研究资源效率至关重要。在免疫研究中,主要目标通常是表征抗体动力学-抗体浓度随时间的变化。然而,抗体动力学的非线性模型对研究设计提出了实质性的挑战,特别是需要提供有关感兴趣参数的信息。我们提出了一个新的框架,以促进设计免疫研究使用简单,可理解的信息。我们假设平均抗体浓度遵循β密度的结构形式,直到达到平台。利用最大值的时间和高度以及平台的时间和高度,我们可以独特地确定抗体动力学曲线。使用d -最优性确定最优抽样计划,使用d -效率来比较设计。在跨12个场景的鲁棒性分析中,我们分析了框架对初始信息中错误规范的敏感性。当一次错误指定一个参数时,中位数d效率超过0.95,所有参数的前四分位数大于或等于0.9,突出了框架的鲁棒性。高原高度和峰值时间的不规范对d -效率影响最大。该框架的巨大优势在于,我们只需要来自医学专业人员的直观信息来设计免疫研究,其中确定抗体动力学是主要目标。
本文章由计算机程序翻译,如有差异,请以英文原文为准。

A Practical Framework to Design Immunization Studies Based on the Beta Distribution.

A Practical Framework to Design Immunization Studies Based on the Beta Distribution.

A Practical Framework to Design Immunization Studies Based on the Beta Distribution.

A Practical Framework to Design Immunization Studies Based on the Beta Distribution.

An optimally designed experiment reaches results quicker, at a lower cost, or with fewer observations and is therefore crucial in maximizing resource efficiency in research. In immunization studies, the primary goal is often to characterize antibody kinetics-the change in antibody concentration over time. However, nonlinear models for antibody kinetics present substantial challenges for study design, particularly the need to provide information on the parameters of interest. We propose a novel framework to facilitate the design of immunization studies using simple, understandable information. We assume that the mean antibody concentration follows the structural form of the beta density until reaching a plateau. Using the time and height of the maximum and the time and height of the plateau, we can uniquely determine the antibody kinetics curve. Optimal sampling schedules are determined using D-optimality, with D-efficiency used to compare designs. In a robustness analysis across 12 scenarios, we analyzed the framework's sensitivity to misspecification in the initial information. When misspecifying one parameter at a time, the median D-efficiencies exceeded 0.95 and the first quartiles were greater than or equal to 0.9 for all parameters, highlighting the robustness of the framework. Misspecification in the height of the plateau and time of the maximum affected the D-efficiency the most. The great advantage of the framework is that we only need intuitive information from the medical professionals to design an immunization study, in which determining the antibody kinetics is the main goal.

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来源期刊
Statistics in Medicine
Statistics in Medicine 医学-公共卫生、环境卫生与职业卫生
CiteScore
3.40
自引率
10.00%
发文量
334
审稿时长
2-4 weeks
期刊介绍: The journal aims to influence practice in medicine and its associated sciences through the publication of papers on statistical and other quantitative methods. Papers will explain new methods and demonstrate their application, preferably through a substantive, real, motivating example or a comprehensive evaluation based on an illustrative example. Alternatively, papers will report on case-studies where creative use or technical generalizations of established methodology is directed towards a substantive application. Reviews of, and tutorials on, general topics relevant to the application of statistics to medicine will also be published. The main criteria for publication are appropriateness of the statistical methods to a particular medical problem and clarity of exposition. Papers with primarily mathematical content will be excluded. The journal aims to enhance communication between statisticians, clinicians and medical researchers.
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