{"title":"修正了“精氨酸酶1缺乏症中Pegzilarginase的长期疗效和耐受性：两项国际多中心开放标签扩展研究的结果”。","authors":"","doi":"10.1002/jimd.70087","DOIUrl":null,"url":null,"abstract":"<p> <span>McNutt, M.</span>, <span>Rutsch, F.</span>, <span>Russo, R.S.</span>, <span>Gasperini, S.</span>, <span>Batzios, S.</span>, <span>Teles, E.L.</span>, <span>Brassier, A.</span>, <span>Ganesh, J.</span>, <span>Schulze, A.</span>, <span>Enns, G.M.</span>, <span>Rudebeck, M.</span>, <span>“Long-Term Efficacy and Tolerability of Pegzilarginase in Arginase 1 Deficiency: Results of Two International Multicentre Open-Label Extension Studies</span>.” <i>Journal of Inherited Metabolic Disease</i> <span>48</span>, no. <span>4</span> (<span>2025</span>): e70066. https://doi.org/10.1002/jimd.70066.</p><p>In the Abstract section of this article, the wording incorrectly stated that 6MWT and 2MWT “improved to” certain distances. The correct description should read “improved by,” as the values represent changes from baseline rather than final absolute distances. Similarly, in the Results section, walk test distances were changes from baseline, that is improvements, not final absolute distances. These wording changes do not alter the study's conclusions.</p><p>We apologize for this error.</p>","PeriodicalId":16281,"journal":{"name":"Journal of Inherited Metabolic Disease","volume":"48 5","pages":""},"PeriodicalIF":3.8000,"publicationDate":"2025-09-10","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70087","citationCount":"0","resultStr":"{\"title\":\"Correction to “Long-Term Efficacy and Tolerability of Pegzilarginase in Arginase 1 Deficiency: Results of Two International Multicentre Open-Label Extension Studies”\",\"authors\":\"\",\"doi\":\"10.1002/jimd.70087\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"<p> <span>McNutt, M.</span>, <span>Rutsch, F.</span>, <span>Russo, R.S.</span>, <span>Gasperini, S.</span>, <span>Batzios, S.</span>, <span>Teles, E.L.</span>, <span>Brassier, A.</span>, <span>Ganesh, J.</span>, <span>Schulze, A.</span>, <span>Enns, G.M.</span>, <span>Rudebeck, M.</span>, <span>“Long-Term Efficacy and Tolerability of Pegzilarginase in Arginase 1 Deficiency: Results of Two International Multicentre Open-Label Extension Studies</span>.” <i>Journal of Inherited Metabolic Disease</i> <span>48</span>, no. <span>4</span> (<span>2025</span>): e70066. https://doi.org/10.1002/jimd.70066.</p><p>In the Abstract section of this article, the wording incorrectly stated that 6MWT and 2MWT “improved to” certain distances. The correct description should read “improved by,” as the values represent changes from baseline rather than final absolute distances. Similarly, in the Results section, walk test distances were changes from baseline, that is improvements, not final absolute distances. These wording changes do not alter the study's conclusions.</p><p>We apologize for this error.</p>\",\"PeriodicalId\":16281,\"journal\":{\"name\":\"Journal of Inherited Metabolic Disease\",\"volume\":\"48 5\",\"pages\":\"\"},\"PeriodicalIF\":3.8000,\"publicationDate\":\"2025-09-10\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70087\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"Journal of Inherited Metabolic Disease\",\"FirstCategoryId\":\"3\",\"ListUrlMain\":\"https://onlinelibrary.wiley.com/doi/10.1002/jimd.70087\",\"RegionNum\":2,\"RegionCategory\":\"医学\",\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"Q1\",\"JCRName\":\"ENDOCRINOLOGY & METABOLISM\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"Journal of Inherited Metabolic Disease","FirstCategoryId":"3","ListUrlMain":"https://onlinelibrary.wiley.com/doi/10.1002/jimd.70087","RegionNum":2,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"Q1","JCRName":"ENDOCRINOLOGY & METABOLISM","Score":null,"Total":0}
引用次数: 0
摘要
McNutt， M., Rutsch， F., Russo, r.s., Gasperini， S., Batzios， S., Teles， E.L, Brassier， A., Ganesh， J., Schulze， A., Enns, g.m., Rudebeck， M.，“精氨酸酶1缺乏症中聚乙二醇精氨酸酶的长期疗效和耐受性：两个国际多中心开放标签扩展研究的结果。”遗传代谢疾病杂志48，第2期。4 (2025): e70066。https://doi.org/10.1002/jimd.70066.In这篇文章的摘要部分，措辞错误地指出，6MWT和2MWT“改进到”一定距离。正确的描述应该是“改进的”，因为这些值代表的是基线的变化，而不是最终的绝对距离。同样，在结果部分，步行测试距离是基线的变化，这是改进，而不是最终的绝对距离。这些措辞的改变不会改变研究的结论。我们为这个错误道歉。
Correction to “Long-Term Efficacy and Tolerability of Pegzilarginase in Arginase 1 Deficiency: Results of Two International Multicentre Open-Label Extension Studies”
McNutt, M., Rutsch, F., Russo, R.S., Gasperini, S., Batzios, S., Teles, E.L., Brassier, A., Ganesh, J., Schulze, A., Enns, G.M., Rudebeck, M., “Long-Term Efficacy and Tolerability of Pegzilarginase in Arginase 1 Deficiency: Results of Two International Multicentre Open-Label Extension Studies.” Journal of Inherited Metabolic Disease48, no. 4 (2025): e70066. https://doi.org/10.1002/jimd.70066.
In the Abstract section of this article, the wording incorrectly stated that 6MWT and 2MWT “improved to” certain distances. The correct description should read “improved by,” as the values represent changes from baseline rather than final absolute distances. Similarly, in the Results section, walk test distances were changes from baseline, that is improvements, not final absolute distances. These wording changes do not alter the study's conclusions.
期刊介绍：
The Journal of Inherited Metabolic Disease (JIMD) is the official journal of the Society for the Study of Inborn Errors of Metabolism (SSIEM). By enhancing communication between workers in the field throughout the world, the JIMD aims to improve the management and understanding of inherited metabolic disorders. It publishes results of original research and new or important observations pertaining to any aspect of inherited metabolic disease in humans and higher animals. This includes clinical (medical, dental and veterinary), biochemical, genetic (including cytogenetic, molecular and population genetic), experimental (including cell biological), methodological, theoretical, epidemiological, ethical and counselling aspects. The JIMD also reviews important new developments or controversial issues relating to metabolic disorders and publishes reviews and short reports arising from the Society''s annual symposia. A distinction is made between peer-reviewed scientific material that is selected because of its significance for other professionals in the field and non-peer- reviewed material that aims to be important, controversial, interesting or entertaining (“Extras”).
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