在癌症中靶向TRIB3-MYC轴:机制见解和治疗中断策略。

IF 2.7 3区 医学 Q2 ONCOLOGY
Emadeldin M Kamel, Sulaiman A Alsalamah, Ahmed A Allam, Noha A Ahmed, Faris F Aba Alkhayl, Al Mokhtar Lamsabhi
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引用次数: 0

摘要

致癌转录因子MYC在大多数人类癌症中驱动增殖、代谢和治疗耐药,但其巨大的核蛋白-蛋白界面长期以来阻碍了直接药物的发现。一个关键的突破是鉴定出tribles pseudokinase 3 (TRIB3)是一个高亲和力的支架,它结合MYC的螺旋-环-螺旋/亮氨酸拉链区,阻断e3 -泛素连接酶UBE3B标记关键赖氨酸,从而延长MYC蛋白的半衰期,同时增强MYC- max的转录输出。这篇综述整合了结构、生化和体内数据,以显示TRIB3基因缺失或药理学清除如何破坏MYC水平,沉默其基因程序,并抑制b细胞淋巴瘤和特定实体瘤的肿瘤生长。我们详细介绍了两种不同的实体肿瘤回路:(i) KRAS-或egfr -突变型肺腺癌中诱导的TRIB3过载,当依维莫司加人参苷Rh2抑制mTOR时,会引发致命的细胞凋亡;(ii)乳腺癌中VHL控制的UBE3B丰度,其中VHL的缺失使肿瘤依赖TRIB3屏蔽来维持MYC信号传导。新兴的治疗方法包括螺旋状和钉接肽,如PCM4,片段衍生的小分子,靶向TRIB3上独特的以glu344为中心的口袋,以及PROTAC降解物,可以消除TRIB3或劫持它来破坏MYC。当与dna损伤剂、BET或CDK7抑制剂或连接酶恢复策略联合使用时,这些干扰物在临床前模型中产生显著的协同作用。剩余的转化挑战——高效的细胞内递送、生物标志物引导的患者选择和脱靶监测——越来越容易处理,这要归功于肽制剂的进步、人工智能加速筛选和靶向降解物的既定调控途径。总的来说,目前的证据表明TRIB3-MYC界面是一个可用药的阿喀琉斯之踵,是临床长期寻求的直接阻断MYC的现实途径。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Targeting the TRIB3-MYC axis in cancer: mechanistic insights and therapeutic disruption strategies.

The oncogenic transcription factor MYC drives proliferation, metabolism, and therapy resistance in the majority of human cancers, yet its large, nuclear protein-protein interface has long frustrated direct drug discovery. A pivotal breakthrough was the identification of Tribbles pseudokinase 3 (TRIB3) as a high-affinity scaffold that binds the helix-loop-helix/leucine zipper region of MYC, blocks the E3-ubiquitin-ligase, UBE3B, from tagging critical lysines, and thereby prolongs MYC protein half-life while enhancing MYC-MAX transcriptional output. This review integrates structural, biochemical, and in vivo data to show how genetic deletion or pharmacological eviction of TRIB3 collapses MYC levels, silences its gene program, and suppresses tumor growth in B-cell lymphomas and selected solid tumors. We detail two distinct solid-tumor circuits: (i) inducible TRIB3 overload in KRAS- or EGFR-mutant lung adenocarcinoma that triggers lethal paraptosis when mTOR is inhibited by everolimus plus ginsenoside Rh2; (ii) VHL-controlled UBE3B abundance in breast carcinoma, where loss of VHL renders tumors dependent on TRIB3 shielding for sustained MYC signaling. Emerging therapeutics include helix-mimetic and stapled peptides such as PCM4, fragment-derived small molecules that target a unique Glu344-centered pocket on TRIB3, and PROTAC degraders that either eliminate TRIB3 or hijack it to destroy MYC. When combined with DNA-damaging agents, BET or CDK7 inhibitors, or ligase-restoring strategies, these disruptors produce marked synergy in preclinical models. Remaining translational challenges-efficient intracellular delivery, biomarker-guided patient selection, and off-target surveillance-are increasingly tractable thanks to advances in peptide formulation, AI-accelerated screening, and established regulatory paths for targeted degraders. Collectively, current evidence positions the TRIB3-MYC interface as a druggable Achilles' heel and a realistic gateway to long-sought direct MYC blockade in the clinic.

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来源期刊
CiteScore
7.60
自引率
0.00%
发文量
121
审稿时长
1 months
期刊介绍: The development of new anticancer agents is one of the most rapidly changing aspects of cancer research. Investigational New Drugs provides a forum for the rapid dissemination of information on new anticancer agents. The papers published are of interest to the medical chemist, toxicologist, pharmacist, pharmacologist, biostatistician and clinical oncologist. Investigational New Drugs provides the fastest possible publication of new discoveries and results for the whole community of scientists developing anticancer agents.
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