Jesman Punian, Morgan Ehman, Deirdre Weymann, Dean A Regier
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引用次数: 0
摘要
慢性淋巴细胞白血病(CLL)是一种常见的、无法治愈的白血病。CLL的精确治疗使用基因检测,使治疗选择与患者特征一致。保险公司对精确CLL治疗的报销不平衡,部分原因是成本效益的证据不确定。本综述调查了目前精确治疗CLL的成本效益证据,并确定了未来研究的领域。我们对2024年10月前发表的PubMed、Embase和Web of Science中收录的精确CLL治疗的经济评估进行了范围审查。共检索到8篇文章。研究检查了不同的患者群体、治疗方案和分层策略。四项研究(50%)仅关注del(17p)和/或TP53突变亚组。三项研究(38%)分析了治疗和基因检测的成本和结果,而62%的研究没有包括基因检测的成本和结果。所有研究均从已发表的试验中获得临床模型参数。五项研究(63%)报告说,精确的CLL治疗可能具有成本效益,愿意支付的阈值从26,489美元/QALY到130,477美元/QALY。未来的研究应侧重于生成真实世界的数据,扩大分析范围以包括社会视角,并探索分布影响,以便在确定其成本效益时更有效地解决精确CLL治疗的异质性。
A scoping review of the cost-effectiveness of precision treatment in chronic lymphocytic leukemia.
Chronic lymphocytic leukemia (CLL) is a common, incurable leukemia. Precision treatment for CLL uses genetic testing to align therapeutic selection with patient characteristics. Insurers are uneven in their reimbursement of precision CLL treatment, partly due to uncertain evidence of cost-effectiveness. This review surveys the current cost-effectiveness evidence for precision CLL treatment and identifies areas for future research. We conducted a scoping review of economic evaluations of precision CLL treatments indexed in PubMed, Embase, and Web of Science and published by October 2024. Eight articles were retrieved. Studies examined heterogeneous patient populations, treatment regimens, and stratification strategies. Four studies (50%) focused on subgroups with del(17p) and/or TP53 mutations only. Three studies (38%) analyzed the costs and outcomes of both treatment and genetic testing, while 62% did not include the cost or outcomes of genetic testing. All studies obtained clinical model parameters from published trials. Five studies (63%) reported that precision CLL treatment was likely cost-effective at willingness to pay thresholds ranging from $26,489/QALY to $130,477/QALY. Future research should focus on generating real-world data, broadening the scope of analysis to include societal perspectives, and exploring distributional impacts to more effectively address the heterogeneity of precision CLL treatments when determining their cost-effectiveness.