{"title":"随机化技术对前后设计模型性能的影响。","authors":"Xinlin Lu, Yahui Zhang, Samuel S Wu, Guogen Shan","doi":"10.1186/s12874-025-02632-z","DOIUrl":null,"url":null,"abstract":"<p><p>Pre-post designs are widely used in clinical trials and experimental studies to assess the effectiveness of treatments. Common statistical methods for analyzing pre-post data include analysis of variance (ANOVA) using post-treatment or the change from baseline, analysis of covariance (ANCOVA) with homogeneous or heterogeneous slopes, and linear mixed models (LMM). While numerous studies have compared these methods, limited studies have investigated the impact of adjusting for influential baseline covariates under different randomization approaches. In this study, we conducted a series of comprehensive simulation studies to investigate the impact of adjusting baseline covariates under several randomization approaches: simple randomization, stratified block randomization, and covariate adaptive randomization using the minimization method by Pocock and Simon. Results demonstrated that when no covariates were considered in the randomization approach, the two ANCOVA methods always have good performance. Adjusting for relevant baseline covariates led to substantial power gains, with the extent of these gains depending on the size of the covariate effects and the randomization approach employed. Stratified block randomization and covariate adaptive randomization consistently outperformed simple randomization in terms of power gains after adjusting for covariates, with covariate adaptive randomization becoming more superior as the number of covariates increased.</p>","PeriodicalId":9114,"journal":{"name":"BMC Medical Research Methodology","volume":"25 1","pages":"176"},"PeriodicalIF":3.9000,"publicationDate":"2025-07-19","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"https://www.ncbi.nlm.nih.gov/pmc/articles/PMC12276662/pdf/","citationCount":"0","resultStr":"{\"title\":\"The impact of randomization techniques on the performance of pre-post design models.\",\"authors\":\"Xinlin Lu, Yahui Zhang, Samuel S Wu, Guogen Shan\",\"doi\":\"10.1186/s12874-025-02632-z\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"<p><p>Pre-post designs are widely used in clinical trials and experimental studies to assess the effectiveness of treatments. Common statistical methods for analyzing pre-post data include analysis of variance (ANOVA) using post-treatment or the change from baseline, analysis of covariance (ANCOVA) with homogeneous or heterogeneous slopes, and linear mixed models (LMM). While numerous studies have compared these methods, limited studies have investigated the impact of adjusting for influential baseline covariates under different randomization approaches. In this study, we conducted a series of comprehensive simulation studies to investigate the impact of adjusting baseline covariates under several randomization approaches: simple randomization, stratified block randomization, and covariate adaptive randomization using the minimization method by Pocock and Simon. Results demonstrated that when no covariates were considered in the randomization approach, the two ANCOVA methods always have good performance. Adjusting for relevant baseline covariates led to substantial power gains, with the extent of these gains depending on the size of the covariate effects and the randomization approach employed. Stratified block randomization and covariate adaptive randomization consistently outperformed simple randomization in terms of power gains after adjusting for covariates, with covariate adaptive randomization becoming more superior as the number of covariates increased.</p>\",\"PeriodicalId\":9114,\"journal\":{\"name\":\"BMC Medical Research Methodology\",\"volume\":\"25 1\",\"pages\":\"176\"},\"PeriodicalIF\":3.9000,\"publicationDate\":\"2025-07-19\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"https://www.ncbi.nlm.nih.gov/pmc/articles/PMC12276662/pdf/\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"BMC Medical Research Methodology\",\"FirstCategoryId\":\"3\",\"ListUrlMain\":\"https://doi.org/10.1186/s12874-025-02632-z\",\"RegionNum\":3,\"RegionCategory\":\"医学\",\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"Q1\",\"JCRName\":\"HEALTH CARE SCIENCES & SERVICES\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"BMC Medical Research Methodology","FirstCategoryId":"3","ListUrlMain":"https://doi.org/10.1186/s12874-025-02632-z","RegionNum":3,"RegionCategory":"医学","ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"Q1","JCRName":"HEALTH CARE SCIENCES & SERVICES","Score":null,"Total":0}
The impact of randomization techniques on the performance of pre-post design models.
Pre-post designs are widely used in clinical trials and experimental studies to assess the effectiveness of treatments. Common statistical methods for analyzing pre-post data include analysis of variance (ANOVA) using post-treatment or the change from baseline, analysis of covariance (ANCOVA) with homogeneous or heterogeneous slopes, and linear mixed models (LMM). While numerous studies have compared these methods, limited studies have investigated the impact of adjusting for influential baseline covariates under different randomization approaches. In this study, we conducted a series of comprehensive simulation studies to investigate the impact of adjusting baseline covariates under several randomization approaches: simple randomization, stratified block randomization, and covariate adaptive randomization using the minimization method by Pocock and Simon. Results demonstrated that when no covariates were considered in the randomization approach, the two ANCOVA methods always have good performance. Adjusting for relevant baseline covariates led to substantial power gains, with the extent of these gains depending on the size of the covariate effects and the randomization approach employed. Stratified block randomization and covariate adaptive randomization consistently outperformed simple randomization in terms of power gains after adjusting for covariates, with covariate adaptive randomization becoming more superior as the number of covariates increased.
期刊介绍:
BMC Medical Research Methodology is an open access journal publishing original peer-reviewed research articles in methodological approaches to healthcare research. Articles on the methodology of epidemiological research, clinical trials and meta-analysis/systematic review are particularly encouraged, as are empirical studies of the associations between choice of methodology and study outcomes. BMC Medical Research Methodology does not aim to publish articles describing scientific methods or techniques: these should be directed to the BMC journal covering the relevant biomedical subject area.