[CRISPR/Cas9技术在嵌合抗原受体T细胞治疗血液恶性肿瘤中的应用策略研究进展]。

Q3 Medicine
Y W Wang, Y M Tang
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引用次数: 0

摘要

嵌合抗原受体(CAR) t细胞疗法在治疗复发/难治性b细胞恶性肿瘤方面取得突破。然而,它仍然面临着挑战,包括复杂的制造工艺、有限的适应症、t细胞衰竭和治疗效果的持久性不足。CRISPR/Cas9是一种高效且相对简单的基因编辑技术,为克服这些限制提供了新的途径。本文简要概述了CRISPR/Cas9的工作机制,重点介绍了其在开发通用CAR - t细胞、增强t细胞功能以及将CAR - t细胞治疗扩展到t细胞和髓性白血病等方面的最新应用和临床实践。此外,本综述还重点介绍了过去两年来为提高CRISPR/Cas9系统的编辑精度、传递效率和安全性而开发的优化策略,旨在为CAR - t细胞治疗的优化设计和临床应用提供见解。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
[Advances in the application strategies of CRISPR/Cas9 technology in chimeric antigen receptor T cell therapy for hematological malignancies].

Chimeric antigen receptor (CAR) T-cell therapy has achieved breakthroughs in treating relapsed/refractory B-cell malignancies. However, it still faces challenges, including complex manufacturing processes, limited indications, T-cell exhaustion, and insufficient durability of therapeutic efficacy. CRISPR/Cas9, a highly efficient and relatively simple gene-editing technology, offers new avenues for overcoming these limitations. This review briefly outlines the working mechanism of CRISPR/Cas9 and focuses on its recent applications and clinical practices in developing universal CAR T-cells, enhancing T-cell function, and extending CAR T-cell therapy to T-cell and myeloid leukemias. Furthermore, this review highlights optimization strategies developed over the past two years to enhance the editing precision, delivery efficiency, and safety of the CRISPR/Cas9 system, aiming to provide insights for the optimal design and clinical application of CAR T-cell therapy.

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CiteScore
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