非恶性疾病的精确移植和细胞治疗——前进的道路。

IF 3.8 2区医学 Q1 HEMATOLOGY

British Journal of Haematology Pub Date : 2025-07-05 DOI:10.1111/bjh.20245

Madhavi Lakkaraja, K Scott Baker

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引用次数: 0

摘要

接受造血干细胞移植（HCT）和非恶性疾病细胞治疗的患者数量正在稳步增加，更多的遗传疾病被发现，新的基因治疗产品被用于各种适应症。通过结合个体化治疗、新颖的移植物操作技术、采用尖端方法监测HCT后反应以及提供卓越的生存护理，我们可以为这些患者实现良好的生存和改善的生活质量。

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Precision transplant and cell therapies for non-malignant disorders-The path forward.

The number of patients undergoing haematopoietic stem cell transplant (HCT) and cell therapies for non-malignant disorders is steadily increasing with more genetic diseases being identified and newer gene therapy products being introduced for various indications. By combining individualized conditioning, novel graft manipulation techniques, using cutting edge methods to monitor post HCT response and offering exceptional survivorship care, one can achieve excellent survival and improved quality of life for these patients.

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来源期刊

British Journal of Haematology 医学-血液学

CiteScore

8.60

自引率

4.60%

发文量

565

审稿时长

1 months

期刊介绍： The British Journal of Haematology publishes original research papers in clinical, laboratory and experimental haematology. The Journal also features annotations, reviews, short reports, images in haematology and Letters to the Editor.