眼科基因治疗策略的现状及展望。

IF 2 3区 生物学 Q3 BIOTECHNOLOGY & APPLIED MICROBIOLOGY
Julia B Krajewska, Arleta Waszczykowska
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引用次数: 0

摘要

基因疗法最近成为治疗以前无法治愈或管理不善的疾病的有希望的策略。这些希望在眼科尤其高,因为眼睛被认为特别适合基因治疗。基因治疗产品的扩大可能会改变临床治疗过程,给许多患者带来新的机会。在这篇综述中,我们讨论了治疗的可能性和递送方法以及与基因治疗相关的挑战和不确定性。我们介绍了遗传和获得性疾病在这一领域的研究,总结了目前眼科基因治疗的趋势,并指出了未来的发展方向。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Gene therapy strategies in ophthalmology-an overview of current developments and future prospects.

Gene therapies have recently emerged as promising strategies for treatment of previously incurable or poorly managed diseases. These hopes are particularly high in ophthalmology, as the eye is considered exceptionally suited for gene therapy. Expansion of gene therapy products may change the clinical course of treatment and give new chances to many patients. In this review, we address treatment possibilities and delivery methods as well as challenges and uncertainties related to gene therapy. We present inherited and acquired diseases which are subject to studies within this area, summarize current trends in ocular gene therapy, and indicate the future directions.

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来源期刊
Journal of Applied Genetics
Journal of Applied Genetics 生物-生物工程与应用微生物
CiteScore
4.30
自引率
4.20%
发文量
62
审稿时长
6-12 weeks
期刊介绍: The Journal of Applied Genetics is an international journal on genetics and genomics. It publishes peer-reviewed original papers, short communications (including case reports) and review articles focused on the research of applicative aspects of plant, human, animal and microbial genetics and genomics.
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