HbE/ β -地中海贫血和α -地中海贫血患者的生存和地中海贫血相关并发症:泰国一项为期10年的纵向研究

IF 5.1 2区 医学 Q1 HEMATOLOGY
Nattiya Teawtrakul, Arunee Jetsrisuparb, Saranya Pongudom, Kanchana Chansung, Chittima Sirijerachai, Supan Fucharoen
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引用次数: 0

摘要

尽管地中海贫血的治疗取得了进展,但存活率和并发症因基因型而有很大差异。本研究评估了泰国东北部地中海贫血患者的生存结局和相关并发症。2012年10月至2023年9月的一项纵向队列研究纳入了在斯利那加林德和乌东他尼医院就诊的年龄≥10岁(中位数:31岁,范围:20-74岁)的患者。Cox回归分析确定了生存和并发症的预测因素。380例入组患者中,340例完成随访。10年间,39例(11.4%)患者死亡,主要死于心血管并发症(61.5%),中位年龄为45岁(范围:22-72岁)。患者分为HbE/β-地中海贫血、HbH/HbHCS伴HbE突变和HbH/HbHCS。HbE/β-地中海贫血(55.9%)和HbH/HbHCS伴HbE突变(58.3%)的60岁生存率低于HbH/HbHCS (79.6%, p = 0.08)。死亡率的重要预测因素包括心血管并发症(HR 2.4;95% ci, 1.01-5.5;p = 0.04),复发性细菌感染(HR 7.6;95% ci, 3.1-18.8;p 2500 ng/mL;人力资源2.0;95% ci, 1.01-3.9;p = 0.04)。心血管并发症、复发性细菌感染和高铁蛋白水平显著影响地中海贫血患者的生存。缺失型α -地中海贫血患者的生存率更高,而HbE/β-地中海贫血和非缺失型α -地中海贫血或共遗传HbE突变的预后较差,强调了基因型特异性管理策略的必要性。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Survival and thalassaemia-related complications in HbE/beta-thalassaemia and alpha-thalassaemia: A 10-year longitudinal study in Thailand.

Despite advancements in thalassaemia care, survival rates and complications vary significantly by genotype. This study assesses survival outcomes and associated complications in patients with thalassaemia in north-eastern Thailand. A longitudinal cohort study from October 2012 to September 2023 involved patients aged ≥10 years (median: 31 years, range: 20-74) attending Srinagarind and Udonthani Hospitals. Cox regression analyses identified predictors of survival and complications. Of 380 enrolled patients, 340 completed follow-up. Over 10 years, 39 patients (11.4%) died, primarily from cardiovascular complications (61.5%), at a median age of 45 years (range: 22-72). Patients were grouped as HbE/β-thalassaemia, HbH/HbHCS with HbE mutation and HbH/HbHCS. Survival at 60 years was lower in HbE/β-thalassaemia (55.9%) and HbH/HbHCS with HbE mutation (58.3%) compared to HbH/HbHCS (79.6%, p = 0.08). Significant predictors of mortality included cardiovascular complications (HR 2.4; 95% CI, 1.01-5.5; p = 0.04), recurrent bacterial infections (HR 7.6; 95% CI, 3.1-18.8; p < 0.001) and elevated ferritin (>2500 ng/mL; HR 2.0; 95% CI, 1.01-3.9; p = 0.04). Cardiovascular complications, recurrent bacterial infections and high ferritin levels significantly influence survival in thalassaemia patients. Deletional alpha-thalassaemia patients had superior survival, while HbE/β-thalassaemia and non-deletional alpha-thalassaemia or co-inherited HbE mutation had poorer outcomes, underscoring the need for genotype-specific management strategies.

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来源期刊
CiteScore
8.60
自引率
4.60%
发文量
565
审稿时长
1 months
期刊介绍: The British Journal of Haematology publishes original research papers in clinical, laboratory and experimental haematology. The Journal also features annotations, reviews, short reports, images in haematology and Letters to the Editor.
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