腺瘤性息肉病的遗传学、基因组学及临床特征。

IF 2 4区 医学 Q3 GENETICS & HEREDITY
Jihoon E Joo, Julen Viana-Errasti, Daniel D Buchanan, Laura Valle
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引用次数: 0

摘要

腺瘤性息肉病综合征是一种遗传性疾病,其特征是胃肠道,特别是结肠和直肠的多发性腺瘤的发展,显著增加结直肠癌的风险,在某些情况下,结外恶性肿瘤。这些综合征是由参与Wnt信号传导和DNA修复的基因中的种系致病变异(pv)引起的。主要的常染色体显性性腺瘤性息肉病综合征包括家族性腺瘤性息肉病(FAP)和聚合酶校对相关息肉病(PPAP),分别由APC和POLE和POLD1基因中的种系pv引起。常染色体隐性综合征包括DNA错配修复基因MLH1、MSH2、MSH6、PMS2、MSH3可能还有MLH3中的双等位基因PVs,以及碱基切除修复基因MUTYH、NTHL1和MBD4中的双等位基因PVs。这篇综述深入讨论了遗传性腺瘤性息肉病综合征的遗传和分子机制、临床表现、肿瘤突变特征以及相关癌症治疗的新方法。本文描述了基因检测的考虑因素,包括合子后嵌合现象、非编码pv、未知意义变异的解释以及与隐性基因中单等位基因变异相关的癌症风险。尽管在基因检测和最近鉴定新的腺瘤性息肉病基因方面取得了进展,但许多多发性腺瘤病例仍然无法从遗传学上解释。非遗传因素,包括环境风险因素、先前的肿瘤治疗和在肠道中定植的细菌基因毒素——特别是产生大肠杆菌素的大肠杆菌——已经成为另一种致病机制。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Genetics, genomics and clinical features of adenomatous polyposis.

Adenomatous polyposis syndromes are hereditary conditions characterised by the development of multiple adenomas in the gastrointestinal tract, particularly in the colon and rectum, significantly increasing the risk of colorectal cancer and, in some cases, extra-colonic malignancies. These syndromes are caused by germline pathogenic variants (PVs) in genes involved in Wnt signalling and DNA repair. The main autosomal dominant adenomatous polyposis syndromes include familial adenomatous polyposis (FAP) and polymerase proofreading-associated polyposis (PPAP), caused by germline PVs in APC and the POLE and POLD1 genes, respectively. Autosomal recessive syndromes include those caused by biallelic PVs in the DNA mismatch repair genes MLH1, MSH2, MSH6, PMS2, MSH3 and probably MLH3, and in the base excision repair genes MUTYH, NTHL1 and MBD4. This review provides an in-depth discussion of the genetic and molecular mechanisms underlying hereditary adenomatous polyposis syndromes, their clinical presentations, tumour mutational signatures, and emerging approaches for the treatment of the associated cancers. Considerations for genetic testing are described, including post-zygotic mosaicism, non-coding PVs, the interpretation of variants of unknown significance and cancer risks associated with monoallelic variants in the recessive genes. Despite advances in genetic testing and the recent identification of new adenomatous polyposis genes, many cases of multiple adenomas remain genetically unexplained. Non-genetic factors, including environmental risk factors, prior oncologic treatments, and bacterial genotoxins colonising the intestine - particularly colibactin-producing Escherichia coli - have emerged as alternative pathogenic mechanisms.

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来源期刊
Familial Cancer
Familial Cancer 医学-遗传学
CiteScore
4.10
自引率
4.50%
发文量
36
审稿时长
6-12 weeks
期刊介绍: In recent years clinical cancer genetics has become increasingly important. Several events, in particular the developments in DNA-based technology, have contributed to this evolution. Clinical cancer genetics has now matured to a medical discipline which is truly multidisciplinary in which clinical and molecular geneticists work together with clinical and medical oncologists as well as with psycho-social workers. Due to the multidisciplinary nature of clinical cancer genetics most papers are currently being published in a wide variety of journals on epidemiology, oncology and genetics. Familial Cancer provides a forum bringing these topics together focusing on the interests and needs of the clinician. The journal mainly concentrates on clinical cancer genetics. Most major areas in the field shall be included, such as epidemiology of familial cancer, molecular analysis and diagnosis, clinical expression, treatment and prevention, counselling and the health economics of familial cancer.
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