家族性癌症的一系列综述:MMR基因中不确定意义变异的遗传癌症风险:应遵循哪些程序?

IF 2 4区 医学 Q3 GENETICS & HEREDITY
Morghan C Lucas, Thomas Keßler, Florentine Scharf, Verena Steinke-Lange, Barbara Klink, Andreas Laner, Elke Holinski-Feder
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引用次数: 0

摘要

解释错配修复(MMR)基因中的不确定意义变异(VUS)仍然是管理Lynch综合征和其他遗传性癌症综合征的主要挑战。本综述概述了推荐的VUS分类程序,包括专家组织为MMR基因量身定制的基础和专业方法,包括InSiGHT和ClinGen的遗传性结直肠癌/息肉病变异管理专家小组(VCEP)。关键方法包括:(1)功能数据,包括测量MMR熟练程度的直接测定,如体外MMR测定、深度突变扫描和基于MMR细胞的测定,以及甲基化耐受性测定、基于蛋白质组学的方法和RNA测序等技术,所有这些都提供了支持变异致病性的关键功能证据;(2)计算数据/工具,包括计算机元预测器和模型,当与实验证据相结合时,有助于稳健的VUS分类;(3)增强变异检测,通过全基因组测序和长读测序,识别实际的致病变异,检测传统方法遗漏的致病变异。这些策略提高了诊断精度,支持Lynch综合征的临床决策,并建立了一个灵活的框架,可应用于其他omim列出的基因。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
A series of reviews in familial cancer: genetic cancer risk in context variants of uncertain significance in MMR genes: which procedures should be followed?

Interpreting variants of uncertain significance (VUS) in mismatch repair (MMR) genes remains a major challenge in managing Lynch syndrome and other hereditary cancer syndromes. This review outlines recommended VUS classification procedures, encompassing foundational and specialized methodologies tailored for MMR genes by expert organizations, including InSiGHT and ClinGen's Hereditary Colorectal Cancer/Polyposis Variant Curation Expert Panel (VCEP). Key approaches include: (1) functional data, encompassing direct assays measuring MMR proficiency such as in vitro MMR assays, deep mutational scanning, and MMR cell-based assays, as well as techniques like methylation-tolerant assays, proteomic-based approaches, and RNA sequencing, all of which provide critical functional evidence supporting variant pathogenicity; (2) computational data/tools, including in silico meta-predictors and models, which contribute to robust VUS classification when integrated with experimental evidence; and (3) enhanced variant detection to identify the actual causal variant through whole-genome sequencing and long-read sequencing to detect pathogenic variants missed by traditional methods. These strategies improve diagnostic precision, support clinical decision-making for Lynch syndrome, and establish a flexible framework that can be applied to other OMIM-listed genes.

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来源期刊
Familial Cancer
Familial Cancer 医学-遗传学
CiteScore
4.10
自引率
4.50%
发文量
36
审稿时长
6-12 weeks
期刊介绍: In recent years clinical cancer genetics has become increasingly important. Several events, in particular the developments in DNA-based technology, have contributed to this evolution. Clinical cancer genetics has now matured to a medical discipline which is truly multidisciplinary in which clinical and molecular geneticists work together with clinical and medical oncologists as well as with psycho-social workers. Due to the multidisciplinary nature of clinical cancer genetics most papers are currently being published in a wide variety of journals on epidemiology, oncology and genetics. Familial Cancer provides a forum bringing these topics together focusing on the interests and needs of the clinician. The journal mainly concentrates on clinical cancer genetics. Most major areas in the field shall be included, such as epidemiology of familial cancer, molecular analysis and diagnosis, clinical expression, treatment and prevention, counselling and the health economics of familial cancer.
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