基于学习的川崎病 IVIG 抗药性和冠状动脉病变预测模型:技术方面和研究特点综述。

IF 3.4 3区 医学 Q1 PEDIATRICS
Danilo Mirata, Anna Chiara Tiezzi, Lorenzo Buffoni, Ilaria Pagnini, Ilaria Maccora, Edoardo Marrani, Maria Vincenza Mastrolia, Gabriele Simonini, Teresa Giani
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引用次数: 0

摘要

川崎病是一种常见的儿童血管炎,冠状动脉病变(CALs)是其最严重的并发症。早期识别高风险患者,包括那些对一线治疗有耐药性的患者,对于指导个性化治疗方法至关重要。鉴于当前评分系统的可靠性有限,人们对基于机器学习算法和人工智能(AI)的新预测模型的开发越来越感兴趣。人工智能有可能通过改善患者分层和支持更有针对性的治疗策略来彻底改变KD的管理。本文综述了人工智能在KD患者分层中的最新应用,特别关注模型预测静脉免疫球蛋白耐药性和CALs风险的能力。我们分析了2019年1月至2024年4月期间发表的研究,这些研究纳入了基于人工智能的预测模型。共有21篇论文符合纳入标准,并进行了技术和统计审查;其中90%是在亚洲医院的患者中进行的。大多数研究(18/21;85.7%)为回顾性研究,其中三分之二纳入的患者少于1000例。在研究设计和参数选择上观察到显著的异质性。静脉注射免疫球蛋白耐药性成为基于人工智能预测CALs模型的关键因素。只有5个模型的灵敏度达到了80%,4个研究提供了对底层算法和数据集的访问。目前,样本量小、类别不平衡以及需要多中心验证等挑战限制了基于机器学习的预测模型的临床适用性。人工智能模型的有效性在很大程度上受到数据的数量和质量、标记准确性和训练数据集的完整性的影响。此外,噪声和缺失数据等问题会对模型性能和泛化性产生负面影响。这些限制突出了对模型代码的严格验证和开放访问的需求,以确保透明度和可再现性。协作和数据共享对于改进人工智能算法、改善患者分层和优化治疗策略至关重要。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Learning-Based Models for Predicting IVIG Resistance and Coronary Artery Lesions in Kawasaki Disease: A Review of Technical Aspects and Study Features.

Kawasaki disease (KD) is a common pediatric vasculitis, with coronary artery lesions (CALs) representing its most severe complication. Early identification of high-risk patients, including those with disease resistant to first-line treatments, is essential to guide personalized therapeutic approaches. Given the limited reliability of current scoring systems, there has been growing interest in the development of new prognostic models based on machine learning algorithms and artificial intelligence (AI). AI has the potential to revolutionize the management of KD by improving patient stratification and supporting more targeted treatment strategies. This narrative review examines recent applications of AI in stratifying patients with KD, with a particular focus on the ability of models to predict intravenous immunoglobulin resistance and the risk of CALs. We analyzed studies published between January 2019 and April 2024 that incorporated AI-based predictive models. In total, 21 papers met the inclusion criteria and were subject to technical and statistical review; 90% of these were conducted in patients from Asian hospitals. Most of the studies (18/21; 85.7%) were retrospective, and two-thirds included fewer than 1000 patients. Significant heterogeneity in study design and parameter selection was observed across the studies. Resistance to intravenous immunoglobulin emerged as a key factor in AI-based models for predicting CALs. Only five models demonstrated a sensitivity > 80%, and four studies provided access to the underlying algorithms and datasets. Challenges such as small sample sizes, class imbalance, and the need for multicenter validation currently limit the clinical applicability of machine-learning-based predictive models. The effectiveness of AI models is heavily influenced by the quantity and quality of data, labeling accuracy, and the completeness of the training datasets. Additionally, issues such as noise and missing data can negatively affect model performance and generalizability. These limitations highlight the need for rigorous validation and open access to model code to ensure transparency and reproducibility. Collaboration and data sharing will be essential for refining AI algorithms, improving patient stratification, and optimizing treatment strategies.

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来源期刊
Pediatric Drugs
Pediatric Drugs PEDIATRICS-PHARMACOLOGY & PHARMACY
CiteScore
7.20
自引率
0.00%
发文量
54
审稿时长
>12 weeks
期刊介绍: Pediatric Drugs promotes the optimization and advancement of all aspects of pharmacotherapy for healthcare professionals interested in pediatric drug therapy (including vaccines). The program of review and original research articles provides healthcare decision makers with clinically applicable knowledge on issues relevant to drug therapy in all areas of neonatology and the care of children and adolescents. The Journal includes: -overviews of contentious or emerging issues. -comprehensive narrative reviews of topics relating to the effective and safe management of drug therapy through all stages of pediatric development. -practical reviews covering optimum drug management of specific clinical situations. -systematic reviews that collate empirical evidence to answer a specific research question, using explicit, systematic methods as outlined by the PRISMA statement. -Adis Drug Reviews of the properties and place in therapy of both newer and established drugs in the pediatric population. -original research articles reporting the results of well-designed studies with a strong link to clinical practice, such as clinical pharmacodynamic and pharmacokinetic studies, clinical trials, meta-analyses, outcomes research, and pharmacoeconomic and pharmacoepidemiological studies. Additional digital features (including animated abstracts, video abstracts, slide decks, audio slides, instructional videos, infographics, podcasts and animations) can be published with articles; these are designed to increase the visibility, readership and educational value of the journal’s content. In addition, articles published in Pediatric Drugs may be accompanied by plain language summaries to assist readers who have some knowledge of, but not in-depth expertise in, the area to understand important medical advances.
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