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引用次数: 0
摘要
淀粉样变性是由蛋白质错误折叠和聚集成淀粉样纤维引起的一组复杂疾病。AL 淀粉样变性是最常见的淀粉样变性之一,其特点是浆细胞克隆的轻链逐渐增殖。越来越多的证据有助于我们了解其发病机制、表现和临床过程。对其临床后遗症的进一步认识增加了 AL 淀粉样变性的发病率。多达 70% 的病例会出现肾脏受累,这对患者的生活质量和治疗方案的选择都有影响,因此特别具有挑战性。因此,早期识别其独特的后遗症、进行适当的分期、全面了解治疗方案并平衡其器官毒性,是治疗这种疾病的关键。我们回顾了目前的治疗标准,并讨论了肾病学家在 AL 淀粉样变性的病理生理学、诊断、结果预测和管理方面的新进展。
Light-chain (AL) amyloidosis for nephrologists-treatment standard.
Amyloidosis is a group of complex diseases caused by the misfolding and aggregation of proteins into amyloid fibrils. Light-chain (AL) amyloidosis is one of the most prevalent forms of amyloidosis, characterized by the gradual proliferation of light chains from plasma cell clones. A growing body of evidence has contributed to our understanding of its pathogenesis, presentation and clinical course. Increased recognition of its clinical sequelae has increased the prevalence of AL amyloidosis. Renal involvement, seen in up to 70% of cases, is particularly challenging due to its impact on quality of life and access to treatment options. Thus, early recognition of its unique sequelae, appropriate staging and a comprehensive understanding of treatment options balanced by their organ toxicities are crucial to managing this disease. We review the current treatment standards and discuss novel developments in the pathophysiology, diagnosis, outcome prediction and management of AL amyloidosis for the Nephrologist.
期刊介绍:
Nephrology Dialysis Transplantation (ndt) is the leading nephrology journal in Europe and renowned worldwide, devoted to original clinical and laboratory research in nephrology, dialysis and transplantation. ndt is an official journal of the [ERA-EDTA](http://www.era-edta.org/) (European Renal Association-European Dialysis and Transplant Association). Published monthly, the journal provides an essential resource for researchers and clinicians throughout the world. All research articles in this journal have undergone peer review.
Print ISSN: 0931-0509.