Carlisle Ford Runge , James Campbell , Carlisle P. Runge , Reena V. Kartha
{"title":"经济学、外差因素与罕见病","authors":"Carlisle Ford Runge , James Campbell , Carlisle P. Runge , Reena V. Kartha","doi":"10.1016/j.rare.2024.100036","DOIUrl":null,"url":null,"abstract":"<div><p>Special combined efforts addressing rare diseases should apply economic principles and methods to maximize returns to research and investment. Four opportunities exist: (1) exploiting treatment spillovers; (2) encouraging institutional networking and knowledge-sharing; (3) recognizing shared molecular and genetic etiologies; (4) organizing resulting clusters and baskets for scaling trials, research, diagnosis and treatment.</p></div>","PeriodicalId":101058,"journal":{"name":"Rare","volume":"2 ","pages":"Article 100036"},"PeriodicalIF":0.0000,"publicationDate":"2024-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"https://www.sciencedirect.com/science/article/pii/S295000872400019X/pdfft?md5=e96d4097c41e3bb196c6eadec23f730a&pid=1-s2.0-S295000872400019X-main.pdf","citationCount":"0","resultStr":"{\"title\":\"Economics, externalities and rare disease\",\"authors\":\"Carlisle Ford Runge , James Campbell , Carlisle P. Runge , Reena V. Kartha\",\"doi\":\"10.1016/j.rare.2024.100036\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"<div><p>Special combined efforts addressing rare diseases should apply economic principles and methods to maximize returns to research and investment. Four opportunities exist: (1) exploiting treatment spillovers; (2) encouraging institutional networking and knowledge-sharing; (3) recognizing shared molecular and genetic etiologies; (4) organizing resulting clusters and baskets for scaling trials, research, diagnosis and treatment.</p></div>\",\"PeriodicalId\":101058,\"journal\":{\"name\":\"Rare\",\"volume\":\"2 \",\"pages\":\"Article 100036\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2024-01-01\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"https://www.sciencedirect.com/science/article/pii/S295000872400019X/pdfft?md5=e96d4097c41e3bb196c6eadec23f730a&pid=1-s2.0-S295000872400019X-main.pdf\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"Rare\",\"FirstCategoryId\":\"1085\",\"ListUrlMain\":\"https://www.sciencedirect.com/science/article/pii/S295000872400019X\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"\",\"JCRName\":\"\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"Rare","FirstCategoryId":"1085","ListUrlMain":"https://www.sciencedirect.com/science/article/pii/S295000872400019X","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}
Special combined efforts addressing rare diseases should apply economic principles and methods to maximize returns to research and investment. Four opportunities exist: (1) exploiting treatment spillovers; (2) encouraging institutional networking and knowledge-sharing; (3) recognizing shared molecular and genetic etiologies; (4) organizing resulting clusters and baskets for scaling trials, research, diagnosis and treatment.