CACNA1E 发育和癫痫性脑病中的癫痫发作和运动障碍:一枚硬币的两面还是两枚不同硬币的同一面?

IF 1.9 4区 医学 Q3 CLINICAL NEUROLOGY
Valentina Di Micco, Leonardo Affronte, Marianne Søndergaard Khinchi, Gitte Rønde, Maria Jose Miranda, Trine Bjørg Hammer, Nicola Specchio, Sándor Beniczky, Kern Olofsson, Rikke S. Møller, Elena Gardella
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引用次数: 0

摘要

CACNA1E的致病变体与早发性癫痫和发育性脑病(DEE)有关。严重至极度的全面发育迟缓、早发难治性癫痫发作、严重肌张力低下和巨头畸形是其主要临床特征。携带复发性 CACNA1E 变异 p.(Gly352Arg) 的患者通常会同时出现早发性 DEE、肌张力障碍/运动障碍和挛缩。(Gly352Arg)CACNA1E变异体。她患有严重的 DEE,并伴有非常频繁的耐药性癫痫发作、极度肌张力低下以及肌张力障碍和运动障碍发作。长期的视频脑电图监测记录了她随后在清醒时出现的强直性不对称癫痫发作,以及睡眠时出现的躯干轻度阵发性运动障碍。这是首次有文献描述这种疾病的脑电图结果。我们的报告强调了 CACNA1E-DEE 患者皮层和皮层下现象之间可能存在重叠。我们还强调了仔细的电气-临床评估对于正确区分这两种疾病是多么必要,它在 CACNA1E-DEE 患儿的临床评估和适当管理中发挥着重要作用。
本文章由计算机程序翻译,如有差异,请以英文原文为准。

Seizure and movement disorder in CACNA1E developmental and epileptic encephalopathy: Two sides of the same coin or same side of two different coins?

Seizure and movement disorder in CACNA1E developmental and epileptic encephalopathy: Two sides of the same coin or same side of two different coins?

Pathogenic variants in CACNA1E are associated with early-onset epileptic and developmental encephalopathy (DEE). Severe to profound global developmental delay, early-onset refractory seizures, severe hypotonia, and macrocephaly are the main clinical features. Patients harboring the recurrent CACNA1E variant p.(Gly352Arg) typically present with the combination of early-onset DEE, dystonia/dyskinesia, and contractures. We describe a 2-year-and-11-month-old girl carrying the p.(Gly352Arg) CACNA1E variant. She has a severe DEE with very frequent drug-resistant seizures, profound hypotonia, and episodes of dystonia and dyskinesia. Long-term video-EEG-monitoring documented subsequent tonic asymmetric seizures during wakefulness and mild paroxysmal dyskinesias of the trunk out of sleep which were thought to be a movement disorder and instead turned out to be focal hyperkinetic seizures. This is the first documented description of the EEG findings in this disorder. Our report highlights a possible overlap between cortical and subcortical phenomena in CACNA1E-DEE. We also underline how a careful electro-clinical evaluation might be necessary for a correct discernment between the two disorders, playing a fundamental role in the clinical assessment and proper management of children with CACNA1E-DEE.

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来源期刊
Epileptic Disorders
Epileptic Disorders 医学-临床神经学
CiteScore
4.10
自引率
8.70%
发文量
138
审稿时长
6-12 weeks
期刊介绍: Epileptic Disorders is the leading forum where all experts and medical studentswho wish to improve their understanding of epilepsy and related disorders can share practical experiences surrounding diagnosis and care, natural history, and management of seizures. Epileptic Disorders is the official E-journal of the International League Against Epilepsy for educational communication. As the journal celebrates its 20th anniversary, it will now be available only as an online version. Its mission is to create educational links between epileptologists and other health professionals in clinical practice and scientists or physicians in research-based institutions. This change is accompanied by an increase in the number of issues per year, from 4 to 6, to ensure regular diffusion of recently published material (high quality Review and Seminar in Epileptology papers; Original Research articles or Case reports of educational value; MultiMedia Teaching Material), to serve the global medical community that cares for those affected by epilepsy.
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